Can a single gene infusion rebuild failing hearts?

NCT ID NCT04179643

First seen Aug 06, 2026 · Last updated Aug 07, 2026 · Updated 1 time

Summary

This early-stage trial is testing a new gene therapy called AB-1002 in people with advanced heart failure (NYHA Class III). The therapy is given as a single infusion directly into the heart's blood vessels, aiming to deliver a gene that may help heart muscle pump more effectively. The study includes about 11 participants with non-ischemic cardiomyopathy and will measure changes in exercise capacity and heart function over a year, with longer-term follow-up by phone. The goal is to see if this approach is safe and shows promise for improving heart function.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
AB-1002, a gene therapy delivered directly to the heart via a single infusion into the coronary arteries
What this could lead to
If successful, this could lead to a new treatment that improves heart function and quality of life for people with advanced heart failure, potentially reducing the need for more invasive interventions.
What could go wrong
This is an early-phase trial with a small number of participants, so the benefits are uncertain. Gene therapy carries risks such as immune reactions or unintended effects on the heart, and it may not work for everyone.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Minneapolis Heart Foundation Institute

    Minneapolis, Minnesota, 55407, United States

  • The Linder Center for Education and Research at The Christ Hospital

    Cincinnati, Ohio, 45219, United States

  • The Ohio State University

    Columbus, Ohio, 43210, United States

  • University of Wisconsin at Madison

    Madison, Wisconsin, 53792, United States

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