SPINAL MUSCULAR ATROPHY
Clinical trials for SPINAL MUSCULAR ATROPHY explained in plain language.
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New yearly injection could help SMA patients move better
Disease control Recruiting nowThis study tests a new drug called salanersen for people aged 15 to 60 with spinal muscular atrophy (SMA). The drug aims to help the body produce more of a key protein needed for muscle and nerve function. Participants receive one injection into the spinal fluid each year for 5 y…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE3 • Sponsor: Biogen • Aim: Disease control
Last updated May 17, 2026 15:13 UTC
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New implant could replace painful spinal injections for SMA patients
Disease control Recruiting nowThis study tests a new device called ThecaFlex DRx that is implanted under the skin to deliver the SMA drug nusinersen directly into the spinal fluid. It is for people with spinal muscular atrophy who have difficulty with standard spinal injections due to spine problems or other …
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Alcyone Therapeutics, Inc • Aim: Disease control
Last updated May 14, 2026 12:03 UTC
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New hope for SMA babies: drug trial aims to boost motor milestones
Disease control Recruiting nowThis study tests a drug called apitegromab in babies under 2 years old who have spinal muscular atrophy (SMA), a genetic condition that weakens muscles. The goal is to see if the drug can improve motor skills like sitting and crawling. All participants must already be on standard…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE2 • Sponsor: Scholar Rock, Inc. • Aim: Disease control
Last updated May 11, 2026 20:50 UTC
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Shocking muscles back to life: new exercise hope for ALS and SMA patients
Symptom relief Recruiting nowThis study tests a special exercise method using whole-body electrical muscle stimulation (WB-EMS) in adults with neuromuscular diseases like ALS, SMA, and muscular dystrophy. Because these conditions make normal exercise hard, WB-EMS directly triggers muscle contractions without…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: University of Missouri-Columbia • Aim: Symptom relief
Last updated May 15, 2026 11:54 UTC
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New study tracks fatigue in SMA patients on nusinersen
Knowledge-focused Recruiting nowThis study looks at how tired people with spinal muscular atrophy (SMA) feel during daily activities while taking the drug nusinersen. Researchers will use a new questionnaire called the SMA EFFORT to measure fatigue. About 45 adolescents and adults who have been on nusinersen fo…
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: Columbia University • Aim: Knowledge-focused
Last updated May 15, 2026 11:56 UTC
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New study peers inside muscles of kids with SMA
Knowledge-focused Recruiting nowThis study watches how spinal muscular atrophy (SMA) drugs work on muscles and nerve cells in children and teens aged 5 to 20. Researchers will use MRI scans and strength tests to see changes over a year. The goal is to learn more about how these treatments affect the body, not t…
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: St. Jude Children's Research Hospital • Aim: Knowledge-focused
Last updated May 15, 2026 11:54 UTC
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New study tracks hidden changes in kids with spinal muscular atrophy on modern therapies
Knowledge-focused Recruiting nowThis study follows 60 children under 16 with spinal muscular atrophy who are already receiving SMN-restoring treatments. Researchers want to describe the new patterns of disease that emerge with these therapies and test which tools best measure progress. The goal is to improve mo…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Hospices Civils de Lyon • Aim: Knowledge-focused
Last updated May 11, 2026 20:50 UTC
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Spanish SMA study aims to map disease journey in 1,000 patients
Knowledge-focused Recruiting nowThis study will follow up to 1,000 people with spinal muscular atrophy (SMA) in Spain over many years to see how their condition changes over time. Researchers will collect information from routine doctor visits, including motor skills, breathing support, and feeding needs. The g…
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: Fundació Sant Joan de Déu • Aim: Knowledge-focused
Last updated Apr 26, 2026 19:35 UTC