SPINAL MUSCULAR ATROPHY
Clinical trials for SPINAL MUSCULAR ATROPHY explained in plain language.
Never miss a new study
Get alerted when new SPINAL MUSCULAR ATROPHY trials appear
Sign up with your email to follow new studies for SPINAL MUSCULAR ATROPHY, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
New hope for babies with SMA: trial tests Muscle-Strengthening drug
Disease control Recruiting nowThis study is testing an investigational drug called apitegromab in infants under 2 years old who have spinal muscular atrophy (SMA). The main goal is to see how the drug moves through the body, how it affects a specific muscle protein, and if it can improve gross motor skills, l…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE2 • Sponsor: Scholar Rock, Inc. • Aim: Disease control
Last updated Mar 27, 2026 12:39 UTC
-
New drug trial aims to help SMA patients walk farther
Disease control Recruiting nowThis study is testing whether an experimental drug called NMD670 can help adults with spinal muscular atrophy type 3 walk farther and improve muscle strength. Researchers will compare NMD670 against a placebo in 54 participants who can walk at least 50 meters without assistance. …
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE2 • Sponsor: NMD Pharma A/S • Aim: Disease control
Last updated Mar 25, 2026 14:08 UTC
-
Implanted port offers hope for SMA patients who Can't get standard spinal injections
Disease control Recruiting nowThis study is testing a small, implanted port and catheter system designed to deliver medication directly to the spinal fluid for people with spinal muscular atrophy (SMA) who cannot receive standard lumbar puncture injections. The device is intended for patients aged 3 and older…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Alcyone Therapeutics, Inc • Aim: Disease control
Last updated Mar 11, 2026 14:53 UTC
-
Zapping muscles to move: new hope for those who Can't exercise?
Symptom relief Recruiting nowThis study is testing a special type of exercise for people with neuromuscular diseases (like ALS or muscular dystrophy) who often can't do regular workouts. It uses a suit that sends mild electrical signals to make muscles contract, aiming to improve strength, walking, balance, …
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: University of Missouri-Columbia • Aim: Symptom relief
Last updated Mar 30, 2026 14:33 UTC
-
Scientists scan muscles to see how SMA treatments really work
Knowledge-focused Recruiting nowThis study aims to learn how existing spinal muscular atrophy (SMA) medications affect patients' muscles and nerve cells over time. Researchers will observe 24 children and young adults (ages 5-20) with SMA types 2 and 3 who are already taking drugs like Spinraza, Zolgensma, or E…
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: St. Jude Children's Research Hospital • Aim: Knowledge-focused
Last updated Apr 01, 2026 14:41 UTC
-
Scientists map the new face of a treated childhood disease
Knowledge-focused Recruiting nowThis study aims to understand how new, life-changing treatments for spinal muscular atrophy (SMA) are changing the course of the disease in children. Researchers will closely follow 60 children under 16 years old for two years to describe their health, development, and quality of…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Hospices Civils de Lyon • Aim: Knowledge-focused
Last updated Mar 30, 2026 14:32 UTC
-
Scientists probe why SMA patients still feel worn out despite treatment
Knowledge-focused Recruiting nowThis study aims to better understand how people with Spinal Muscular Atrophy experience physical fatigue during their daily activities while receiving nusinersen treatment. Researchers will follow 45 adolescents and adults who have been on stable nusinersen dosing for at least 6 …
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: Columbia University • Aim: Knowledge-focused
Last updated Mar 24, 2026 12:02 UTC
-
Massive spanish study to map SMA journey for 1000 patients
Knowledge-focused Recruiting nowThis study aims to collect long-term health data from 1000 spinal muscular atrophy (SMA) patients across Spain over at least 5 years. Researchers will track how patients' movement abilities, treatments, and overall health change over time in real-world medical settings. The goal …
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: Fundació Sant Joan de Déu • Aim: Knowledge-focused
Last updated Mar 20, 2026 14:48 UTC