Scientists peek inside muscles of kids with SMA to see how drugs really work
NCT ID NCT06532474
First seen Jun 27, 2026 · Last updated Jul 10, 2026 · Updated 2 times
Summary
This study watches how spinal muscular atrophy (SMA) drugs change muscles and nerves in 24 children aged 5 to 20. Using MRI scans, strength tests, and blood samples, researchers track changes over a year. The goal is not to test a new treatment but to better understand how existing therapies affect the body.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Study contacts
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Contact
Email: •••••@•••••
Locations
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St. Jude Children's Research Hospital
RECRUITINGMemphis, Tennessee, 38105, United States
Contact Email: •••••@•••••
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Other studies related to the condition(s) this trial covers.
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