SPINAL MUSCULAR ATROPHY
Clinical trials for SPINAL MUSCULAR ATROPHY explained in plain language.
Never miss a new study
Get alerted when new SPINAL MUSCULAR ATROPHY trials appear
Sign up with your email to follow new studies for SPINAL MUSCULAR ATROPHY, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Two-year safety check for SMA drug in hundreds of patients
Disease control OngoingThis study follows 404 adults and children with spinal muscular atrophy (SMA) who are already taking the approved drug risdiplam (Evrysdi). Researchers will track patients for about two years to monitor the long-term safety of the medication and see how well it continues to work.…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE4 • Sponsor: Genentech, Inc. • Aim: Disease control
Last updated Apr 01, 2026 14:42 UTC
-
Doctors monitor Real-World impact of SMA drug in adults
Disease control OngoingThis study is observing how the approved drug Spinraza (nusinersen) affects adults living with SMA type II, a genetic muscle-weakening condition. Researchers are closely tracking 20 wheelchair-using adults over more than two years to see how their motor skills, strength, breathin…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Centre Hospitalier Universitaire de Nice • Aim: Disease control
Last updated Mar 30, 2026 14:35 UTC
-
New drug aims to build muscle in SMA patients
Disease control OngoingThis study is testing whether a new drug called taldefgrobep alfa can improve muscle function and strength in people with spinal muscular atrophy (SMA). The drug is given as a shot and is designed to block a protein that limits muscle growth. It is being tested in 269 people who …
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE3 • Sponsor: Biohaven Pharmaceuticals, Inc. • Aim: Disease control
Last updated Mar 16, 2026 15:27 UTC
-
New test aims to stop dangerous falls for people with Muscle-Weakening diseases
Diagnosis ENROLLING_BY_INVITATIONThis study aims to create and validate a simple set of physical tests to better predict the risk of falling for people with various nerve and muscle disorders. Researchers will test 108 patients with conditions like muscular dystrophy and ALS using tasks like standing up from a c…
Matched conditions: SPINAL MUSCULAR ATROPHY
Sponsor: LMU Klinikum • Aim: Diagnosis
Last updated Mar 20, 2026 14:47 UTC
-
Can standing wheelchairs help kids join in more?
Knowledge-focused OngoingThis small, early-stage study is exploring whether powered wheelchairs that can lift a child into a standing position help kids with conditions like cerebral palsy or spinal cord injuries participate more in daily activities. Researchers are working with four children in Michigan…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Grand Valley State University • Aim: Knowledge-focused
Last updated Mar 27, 2026 12:40 UTC
-
Motion sensors aim to track progress in SMA babies on new treatments
Knowledge-focused OngoingThis study is testing a new way to measure movement in babies with spinal muscular atrophy (SMA) who are receiving new gene or drug therapies. Researchers will use small, wearable motion sensors on the babies' arms and legs to get a more detailed picture of their motor function. …
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: NA • Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Knowledge-focused
Last updated Mar 23, 2026 15:14 UTC