SPINAL MUSCULAR ATROPHY
Clinical trials for SPINAL MUSCULAR ATROPHY explained in plain language.
Never miss a new study
Get alerted when new SPINAL MUSCULAR ATROPHY trials appear
Sign up with your email to follow new studies for SPINAL MUSCULAR ATROPHY, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Gene therapy injection tested in Real-World fight against debilitating muscle disease
Disease control Not yet recruitingThis study aims to gather real-world evidence on the safety and effectiveness of a one-time spinal injection gene therapy (ITVISMA®) for people with Spinal Muscular Atrophy (SMA). It will follow 36 U.S. participants, aged 2 and older, for at least a year after their treatment to …
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE4 • Sponsor: Novartis Pharmaceuticals • Aim: Disease control
Last updated Mar 27, 2026 12:40 UTC
-
New hope for SMA: yearly injection aims to boost muscle function
Disease control Not yet recruitingThis study is testing a new drug called salanersen (BIIB115) for people aged 15-60 with spinal muscular atrophy (SMA). The goal is to see if it can improve muscle movement and function. It will include people who have never had SMA treatment and those who are switching from the d…
Matched conditions: SPINAL MUSCULAR ATROPHY
Phase: PHASE3 • Sponsor: Biogen • Aim: Disease control
Last updated Mar 23, 2026 15:16 UTC