SPINAL MUSCULAR ATROPHY

Clinical trials for SPINAL MUSCULAR ATROPHY explained in plain language.

Never miss a new study

Get alerted when new SPINAL MUSCULAR ATROPHY trials appear

Sign up with your email to follow new studies for SPINAL MUSCULAR ATROPHY, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.

Our safety recommendation!

By submitting, you agree to our Terms of use

Trials to join now! 10 Not yet recruiting 1 Not yet finished but already full! 10 Completed 14 Terminated 1

New study to track gene Therapy's Real-World impact on spinal muscular atrophy

Disease control Not yet recruiting

This study will follow 36 people with spinal muscular atrophy (SMA) who receive a gene therapy called onasemnogene abeparvovec (ITVISMA) injected into the spinal fluid. The goal is to see how well it works and how safe it is in everyday medical practice. Participants must be at l…

Matched conditions: SPINAL MUSCULAR ATROPHY

Phase: PHASE4 • Sponsor: Novartis Pharmaceuticals • Aim: Disease control

Last updated Jun 27, 2026 13:00 UTC

SPINAL MUSCULAR ATROPHY

Get alerted when new SPINAL MUSCULAR ATROPHY trials appear

New study to track gene Therapy's Real-World impact on spinal muscular atrophy