SPINAL MUSCULAR ATROPHY

Clinical trials for SPINAL MUSCULAR ATROPHY explained in plain language.

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Trials to join now! 8 Not yet recruiting 1 Not yet finished but already full! 8 Completed 11 Terminated 1

New gene therapy for SMA gets Real-World check in U.S. clinics

Disease control Not yet recruiting

This study follows 36 people with spinal muscular atrophy (SMA) who receive a one-time gene therapy (ITVISMA®) injected into the spine. Researchers will track how well it improves movement and what side effects occur in everyday medical practice. The goal is to see if this treatm…

Matched conditions: SPINAL MUSCULAR ATROPHY

Phase: PHASE4 • Sponsor: Novartis Pharmaceuticals • Aim: Disease control

Last updated May 17, 2026 15:14 UTC

SPINAL MUSCULAR ATROPHY

Get alerted when new SPINAL MUSCULAR ATROPHY trials appear

New gene therapy for SMA gets Real-World check in U.S. clinics