New study tracks hidden changes in kids with spinal muscular atrophy on modern therapies

NCT ID NCT06321965

First seen Jan 30, 2026 · Last updated May 09, 2026 · Updated 18 times

Summary

This study follows 60 children under 16 with spinal muscular atrophy who are already receiving SMN-restoring treatments. Researchers want to describe the new patterns of disease that emerge with these therapies and test which tools best measure progress. The goal is to improve monitoring and care, not to test a new treatment.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for SPINAL MUSCULAR ATROPHY are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • CHRU of Brest

    NOT_YET_RECRUITING

    Brest, 29609, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Department of Pediatrics - Neurology and Infectious Diseases Toulouse University Hospital - Children's Hospital

    NOT_YET_RECRUITING

    Toulouse, 31059, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hautepierre Hospital - Mother and Child Hospital

    NOT_YET_RECRUITING

    Strasbourg, 67200, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • I-Motion Pediatric Clinical Trial Platform Armand Trousseau Hospital

    NOT_YET_RECRUITING

    Paris, 75012, France

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Marseille University Hospital - Timone Hospital Department of Pediatric Neurology - Specialized Pediatrics and Child Medicine

    NOT_YET_RECRUITING

    Marseille, 13005, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Pediatric Neurology Swynghedauw Hospital

    NOT_YET_RECRUITING

    Lille, 59037, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Pediatric Neurology and Resuscitation Raymond-Poincare Hospital

    NOT_YET_RECRUITING

    Garche, 92380, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Pediatric Rehabilitation Service - L'Escale Mother and Child Hospital

    RECRUITING

    Bron, Rhone, 69500, France

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.