New implant could help SMA patients who Can't get spinal injections

NCT ID NCT05866419

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This trial tests a new implantable device called ThecaFlex DRx in 90 people with spinal muscular atrophy (SMA) who cannot receive standard spinal injections due to spine problems or other risks. The device is placed under the skin and delivers the medication nusinersen directly into the spinal fluid. Researchers will check if the device works safely and effectively over 12 months.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ThecaFlex DRx System (implantable port and catheter)

What this could lead to

If successful, this device could provide a safer, easier way to deliver life-saving SMA medication to patients who currently cannot receive it due to spine problems.

What could go wrong

This is an early feasibility study with no control group, so results may not confirm the device is better than standard care. Implant surgery carries risks like infection or device malfunction.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

scoliosis spinal muscular atrophy vertebral column disorder

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Barrow Neurological Institute

    RECRUITING

    Phoenix, Arizona, 85013, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Email: •••••@•••••

  • Children's Hospital Orange County

    RECRUITING

    Orange, California, 92868, United States

    Contact Email: •••••@•••••

  • Children's Hospital Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact Email: •••••@•••••

  • Childrens Hospital of the King's Daughters

    RECRUITING

    Norfolk, Virginia, 23510, United States

    Contact Email: •••••@•••••

  • Columbia University Irving Medical Center/NewYork Presbyterian Hospital

    RECRUITING

    New York, New York, 10032, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Helen DeVos Children's Hospital

    RECRUITING

    Grand Rapids, Michigan, 49503, United States

    Contact Email: •••••@•••••

  • Hospital Universitario La Paz

    RECRUITING

    Madrid, Spain

    Contact Email: •••••@•••••

  • Hospital Universitario y Politecnico la Fe de Valencia

    RECRUITING

    Valencia, 46026, Spain

    Contact Email: •••••@•••••

  • Lurie Childrens Hospital

    RECRUITING

    Chicago, Illinois, 60611, United States

    Contact Email: •••••@•••••

    Contact

  • Nemours Children's Hospital, Florida

    RECRUITING

    Orlando, Florida, 32827, United States

    Contact Email: •••••@•••••

  • Penn State Milton S. Hershey Medical Center

    RECRUITING

    Hershey, Pennsylvania, 17033, United States

    Contact Email: •••••@•••••

  • Rady Children's Hospital

    RECRUITING

    San Diego, California, 92037, United States

    Contact Email: •••••@•••••

  • Research Institute of Polish Mother's Memorial Hospital

    RECRUITING

    Lodz, Poland

    Contact Email: •••••@•••••

  • Sheffield Teaching Hospitals NHS Foundation Trust

    RECRUITING

    Sheffield, United Kingdom

    Contact Email: •••••@•••••

  • Specialised Hospital Ludwika Rydygiera

    RECRUITING

    Krakow, Poland

    Contact Email: •••••@•••••

  • Stanford Medical Center

    RECRUITING

    Palo Alto, California, 94301, United States

    Contact Email: •••••@•••••

  • Texas Children's Hospital

    RECRUITING

    Houston, Texas, 77030, United States

    Contact Email: •••••@•••••

  • UH Rainbow Babies and Children's Hospital

    RECRUITING

    Cleveland, Ohio, 44106, United States

    Contact Email: •••••@•••••

  • University of Virginia

    RECRUITING

    Charlottesville, Virginia, 22903, United States

    Contact Email: •••••@•••••

    Contact

  • Universitätsklinikum Essen

    RECRUITING

    Essen, Germany

    Contact Email: •••••@•••••