1,000 SMA patients enrolled in landmark Real-World data study

NCT ID NCT07231549

First seen Jun 26, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This observational study will follow 1,000 people with spinal muscular atrophy (SMA) in Spain over many years. Researchers will collect information on motor skills, breathing support, and feeding needs during routine clinic visits. The goal is to standardize how SMA data is gathered in real-world settings, which could improve care and future research.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

What this could lead to

If successful, this study could provide a clearer picture of how spinal muscular atrophy progresses over time in routine care, helping to improve future treatment guidelines.

What could go wrong

This is an observational study, not a treatment trial, so it won't directly test a new therapy. Results depend on consistent data collection across many hospitals, which can be challenging.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

spinal muscular atrophy

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Hospital Sant Joan de Déu

    RECRUITING

    Esplugues de Llobregat, Spain