New drug PLX038 targets aggressive brain tumors

NCT ID NCT06161519

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tests a drug called PLX038 in adults with brain or spinal cord tumors, including those with changes in the MYC or MYCN genes. The trial has two phases: first, finding the right dose, then checking if it works. Participants receive PLX038 intravenously every three weeks for up to 7 months, with follow-up for up to 5 years.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

PLX038

What this could lead to

If successful, this could provide a new treatment option for certain brain and spinal cord tumors, especially those with MYC or MYCN gene changes.

What could go wrong

This is an early-phase trial (Phase I/II) with a small number of participants, so the drug may not prove effective or safe for wider use. Side effects and risks are still being evaluated.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

brain cancer ependymoma glioblastoma glioma medulloblastoma primary brain neoplasm Recurrence

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • National Institutes of Health Clinical Center

    RECRUITING

    Bethesda, Maryland, 20892, United States

    Contact Email: •••••@•••••