PRADER-WILLI SYNDROME
Clinical trials for PRADER-WILLI SYNDROME explained in plain language.
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Could a diabetes drug help young adults with rare obesity conditions lose weight?
Disease control Recruiting nowThis study is testing a weight-loss medication called tirzepatide in young adults aged 18-26 who have obesity due to Prader-Willi syndrome, hypothalamic obesity, or general causes. Participants will take the drug for one year to see how much weight they lose and how their health …
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE4 • Sponsor: Grace Kim • Aim: Disease control
Last updated May 17, 2026 04:35 UTC
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Gut health boost: could probiotics curb appetite in rare genetic obesity?
Disease control Recruiting nowThis study looks at whether probiotics and prebiotics can safely help control appetite and weight gain in 60 children with Prader-Willi syndrome, a rare genetic condition that causes severe obesity. Researchers will measure changes in body mass index, body fat, and gut bacteria o…
Matched conditions: PRADER-WILLI SYNDROME
Phase: NA • Sponsor: Children's Hospital of Fudan University • Aim: Disease control
Last updated May 14, 2026 12:03 UTC
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New weekly shot hopes to tame genetic obesity
Disease control Recruiting nowThis study tests a new weekly injection called RM-718 in people with obesity, including those with a genetic condition affecting the MC4R pathway (like Prader-Willi syndrome). The main goal is to check the drug's safety and how the body processes it. About 150 participants will t…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE1, PHASE2 • Sponsor: Rhythm Pharmaceuticals, Inc. • Aim: Disease control
Last updated Apr 30, 2026 15:49 UTC
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New drug aims to curb relentless hunger in rare genetic disorder
Symptom relief Recruiting nowThis early-stage trial tests an experimental drug called CSTI-500 in 12 people with Prader-Willi syndrome, a genetic condition that causes constant, extreme hunger. The study aims to see if the drug is safe and can reduce the urge to overeat. Participants aged 13 to 50 will recei…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE2 • Sponsor: ConSynance Therapeutics • Aim: Symptom relief
Last updated May 17, 2026 04:17 UTC
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New hope for sleepiness in Prader-Willi syndrome: drug trial underway
Symptom relief Recruiting nowThis study tests a drug called pitolisant to see if it can reduce severe daytime sleepiness in people with Prader-Willi syndrome, a genetic condition. About 134 participants aged 6 and older will receive either the drug or a placebo, and then all will have the option to take the …
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Harmony Biosciences Management, Inc. • Aim: Symptom relief
Last updated May 14, 2026 12:06 UTC
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Magnetic brain zap targets Out-of-Control hunger in rare disorder
Knowledge-focused Recruiting nowThis study is testing a safe, noninvasive technique called TMS (transcranial magnetic stimulation) to see if it can affect brain areas linked to hunger and fullness in people with Prader-Willi syndrome. Twenty participants will receive TMS and have brain scans before and after. T…
Matched conditions: PRADER-WILLI SYNDROME
Phase: NA • Sponsor: Brigham and Women's Hospital • Aim: Knowledge-focused
Last updated May 15, 2026 11:58 UTC
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Scientists launch Largest-Ever study on rare imprinting disorders
Knowledge-focused Recruiting nowThis study follows 2000 children and adults with rare genetic conditions called imprinting disorders, such as Silver-Russell and Prader-Willi syndromes. Researchers aim to identify common metabolic patterns and health risks like obesity or diabetes. No new treatments are tested; …
Matched conditions: PRADER-WILLI SYNDROME
Sponsor: Institut National de la Santé Et de la Recherche Médicale, France • Aim: Knowledge-focused
Last updated May 14, 2026 12:05 UTC
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New study aims to get adults with intellectual disability moving more
Knowledge-focused Recruiting nowThis study tests a program called PACE that helps adults with intellectual disability become more physically active. About 120 adults, along with their caregivers and coaches, will take part. The program focuses on increasing daily steps and moderate-to-vigorous activity, and the…
Matched conditions: PRADER-WILLI SYNDROME
Phase: NA • Sponsor: University of North Carolina, Chapel Hill • Aim: Knowledge-focused
Last updated May 12, 2026 13:42 UTC
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New registry aims to shed light on rare diseases
Knowledge-focused Recruiting nowThis study is creating a large database to collect information about people with rare diseases like amyloidosis, sarcoidosis, and many others. Researchers will track participants' health, treatments, and outcomes over time to better understand these conditions. The goal is to imp…
Matched conditions: PRADER-WILLI SYNDROME
Sponsor: Hospital Italiano de Buenos Aires • Aim: Knowledge-focused
Last updated May 11, 2026 20:49 UTC