PRADER-WILLI SYNDROME
Clinical trials for PRADER-WILLI SYNDROME explained in plain language.
Never miss a new study
Get alerted when new PRADER-WILLI SYNDROME trials appear
Sign up with your email to follow new studies for PRADER-WILLI SYNDROME, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Experimental drug targets uncontrollable hunger in rare genetic disorder
Disease control OngoingThis study is testing whether a daily injection called setmelanotide can help people with Prader-Willi Syndrome manage their weight and reduce extreme hunger behaviors. About 20 participants aged 6-65 will receive the medication for up to one year while researchers monitor safety…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE2 • Sponsor: Rhythm Pharmaceuticals, Inc. • Aim: Disease control
Last updated Apr 01, 2026 14:42 UTC
-
New drug trial aims to tame uncontrollable hunger in rare genetic disorder
Disease control TerminatedThis study is testing whether ARD-101 can safely help control the extreme, life-threatening hunger experienced by people with Prader-Willi syndrome over a full year. It follows 90 patients who previously participated in a related 12-week trial, asking them to take the medication …
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Aardvark Therapeutics, Inc. • Aim: Disease control
Last updated Mar 27, 2026 12:39 UTC
-
Researchers track safety of rare disease drug in final testing phase
Disease control ENROLLING_BY_INVITATIONThis study is checking the long-term safety of a medication called pitolisant in people with Prader-Willi syndrome, a rare genetic disorder. It's open to about 150 participants who have already taken pitolisant in previous related studies. The main goal is to monitor for any side…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Harmony Biosciences Management, Inc. • Aim: Disease control
Last updated Mar 27, 2026 12:38 UTC
-
Real-World tracking begins for rare genetic disorder treatment
Disease control ENROLLING_BY_INVITATIONThis study is observing 200 patients with Prader-Willi syndrome who are taking the medication VYKAT XR. The main goal is to gather more information about the drug's safety and how patients respond during real-world use. It follows patients who are either starting the treatment or…
Matched conditions: PRADER-WILLI SYNDROME
Sponsor: Soleno Therapeutics, Inc. • Aim: Disease control
Last updated Mar 23, 2026 15:16 UTC
-
New drug trial aims to tame uncontrollable hunger in rare genetic disorder
Symptom relief TerminatedThis study is testing whether an investigational drug called ARD-101 can reduce the extreme, life-threatening hunger (hyperphagia) experienced by people with Prader-Willi syndrome. About 90 participants, aged 7 and older, will take either ARD-101 or a placebo pill daily for 12 we…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Aardvark Therapeutics, Inc. • Aim: Symptom relief
Last updated Mar 30, 2026 14:29 UTC
-
New hope for fighting crippling sleepiness in rare genetic disorder
Symptom relief OngoingThis study is testing whether a medication called pitolisant can safely reduce excessive daytime sleepiness in people with Prader-Willi syndrome (PWS), a rare genetic disorder. About 65 patients aged 6 to 65 will receive either the drug or a placebo for 11 weeks, with an option f…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE2 • Sponsor: Harmony Biosciences Management, Inc. • Aim: Symptom relief
Last updated Mar 25, 2026 14:08 UTC