MYOTONIC DYSTROPHY 1
Clinical trials for MYOTONIC DYSTROPHY 1 explained in plain language.
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New drug trial aims to tame debilitating muscle disease
Disease control Recruiting nowThis early-stage study is testing a new drug called ARO-DM1 in adults with myotonic dystrophy type 1, a genetic disorder that causes progressive muscle weakness and stiffness. The main goal is to see if the drug is safe and how the body processes it. Researchers will also measure…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE1, PHASE2 • Sponsor: Arrowhead Pharmaceuticals • Aim: Disease control
Last updated Apr 01, 2026 14:42 UTC
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New drug trial aims to ease debilitating muscle stiffness
Disease control Recruiting nowThis study is testing an investigational medicine called PGN-EDODM1 in adults with myotonic dystrophy type 1, a genetic disorder that causes progressive muscle weakness and stiffness. Researchers want to see if multiple doses are safe and tolerable, and if they can improve muscle…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE2 • Sponsor: PepGen Inc • Aim: Disease control
Last updated Apr 01, 2026 14:42 UTC
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Common diabetes drug could help control rare Muscle-Wasting disease
Disease control Recruiting nowThis study is testing whether metformin, a medication commonly used for diabetes, can improve muscle function and control symptoms in adults with myotonic dystrophy type 1 (Steinert's disease). Researchers will compare metformin against a placebo in 142 participants over 12 month…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE3 • Sponsor: Assistance Publique - Hôpitaux de Paris • Aim: Disease control
Last updated Mar 30, 2026 14:33 UTC
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Hope for muscle disease: Long-Term drug safety study opens
Disease control Recruiting nowThis study aims to learn about the long-term safety of an experimental drug called PGN-EDODM1 for adults with myotonic dystrophy type 1. It is open only to people who have already received this drug in a previous clinical trial. The main goal is to monitor participants for any si…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE2 • Sponsor: PepGen Inc • Aim: Disease control
Last updated Mar 30, 2026 14:31 UTC
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New drug trial aims to ease debilitating muscle stiffness
Disease control Recruiting nowThis early-stage trial is testing a new drug called ATX-01 in adults with myotonic dystrophy type 1 (DM1), a genetic disorder that causes progressive muscle weakness and stiffness. The main goal is to see if the drug is safe and well-tolerated when given as a single dose or as th…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE1, PHASE2 • Sponsor: ARTHEx Biotech S.L. • Aim: Disease control
Last updated Mar 16, 2026 15:25 UTC
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Massive spanish study launches to map a rare muscle disease
Knowledge-focused Recruiting nowThis study aims to create a detailed national picture of Myotonic Dystrophy Type 1 (DM1) in Spain. It will enroll up to 3,000 people with DM1 to collect their health information over time in a central registry. The goal is to better understand how the disease progresses and to id…
Matched conditions: MYOTONIC DYSTROPHY 1
Sponsor: Fundació Institut Germans Trias i Pujol • Aim: Knowledge-focused
Last updated Apr 02, 2026 07:27 UTC