MYOTONIC DYSTROPHY 1
Clinical trials for MYOTONIC DYSTROPHY 1 explained in plain language.
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Hope for muscle disease: new drug enters final testing phase
Disease control OngoingThis study tests a new medicine called AOC 1001 for people with myotonic dystrophy type 1, a genetic disease that causes muscle weakness and stiffness. About 159 adults with a confirmed diagnosis will receive either the drug or a placebo by IV. The main goal is to see if the drug…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE3 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated May 14, 2026 12:02 UTC
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Hope for DM1: new drug tested for long-term safety
Disease control ENROLLING_BY_INVITATIONThis study looks at the long-term safety and effects of a drug called AOC 1001 in people with myotonic dystrophy type 1 (DM1), a genetic muscle disease. About 230 adults who already took part in earlier AOC 1001 studies will receive the drug intravenously. The main goal is to tra…
Matched conditions: MYOTONIC DYSTROPHY 1
Phase: PHASE3 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated May 11, 2026 20:49 UTC
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500 chinese patients join study to unlock secrets of rare muscle disease
Knowledge-focused ENROLLING_BY_INVITATIONThis study aims to collect health and genetic information from 500 Chinese adults with myotonic dystrophy type 1 (DM1), a rare inherited muscle disorder. Researchers will measure walking speed and daytime sleepiness to see how the disease affects daily life. The goal is to better…
Matched conditions: MYOTONIC DYSTROPHY 1
Sponsor: Huashan Hospital • Aim: Knowledge-focused
Last updated May 15, 2026 11:53 UTC