New hope for muscle stiffness: experimental drug PGN-EDODM1 enters Mid-Stage trial

NCT ID NCT06667453

First seen Jun 24, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study tests an investigational drug called PGN-EDODM1 in 24 adults with myotonic dystrophy type 1, a condition causing muscle stiffness and weakness. Participants receive multiple doses of the drug or a placebo by IV to check safety and how the body processes it. The goal is to see if the drug is safe and tolerable.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

PGN-EDODM1

What this could lead to

If successful, this could point toward a treatment that controls symptoms of myotonic dystrophy type 1, like muscle stiffness and weakness.

What could go wrong

This is an early Phase 2 trial with only 24 participants, so results may not apply to everyone. The drug is still experimental and may not work or could have side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

myotonic dystrophy myotonic dystrophy type 1

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • CIUSSS du Saguenay-Lac-Saint-Jean

    RECRUITING

    Chicoutimi, Quebec, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Montreal Neurological Institute

    RECRUITING

    Montreal, Quebec, H3A 2B4, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Newcastle Upon Tyne Hospitals

    RECRUITING

    Newcastle upon Tyne, NE7 7DN, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Ottawa Hospital Research Institute (OHRI)

    RECRUITING

    Ottawa, Ontario, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Pacific Clinical Research Network Auckland

    ACTIVE_NOT_RECRUITING

    Takapuna, Auckland, 0622, New Zealand

  • Salford Royal Hospital

    RECRUITING

    Salford, England, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University College London Hospitals NHS Foundation Trust

    RECRUITING

    London, UK, United Kingdom

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Calgary

    RECRUITING

    Calgary, Alberta, T2N 4Z6, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••