Hope for DM1: Long-Term safety trial launches for experimental drug

NCT ID NCT07220603

First seen Nov 01, 2025 · Last updated May 15, 2026 · Updated 34 times

Summary

This study looks at the long-term safety of an experimental drug called PGN-EDODM1 for people with myotonic dystrophy type 1 (DM1). It is for those who have already taken the drug in a previous study. About 48 adults will take part, and researchers will track any side effects over time.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • CIUSSS du Saguenay-Lac-Saint-Jean

    RECRUITING

    Saguenay, Canada

    Contact Email: •••••@•••••

  • Ottawa Hospital Research Institute

    RECRUITING

    Ottawa, Ontario, Canada

    Contact Email: •••••@•••••

  • University of Calgary

    RECRUITING

    Calgary, Alberta, T2N 4Z6, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.