DRAVET SYNDROME
Clinical trials for DRAVET SYNDROME explained in plain language.
Never miss a new study
Get alerted when new DRAVET SYNDROME trials appear
Sign up with your email to follow new studies for DRAVET SYNDROME, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
New hope for dravet syndrome: expanded access to seizure drug stiripentol
Disease control APPROVED_FOR_MARKETINGThis program provides expanded access to the drug stiripentol for people with Dravet syndrome, a severe form of epilepsy that causes frequent, hard-to-control seizures. It is open to patients aged 6 months and older who have not responded to other treatments. The goal is to help …
Matched conditions: DRAVET SYNDROME
Sponsor: Children's Hospital Medical Center, Cincinnati • Aim: Disease control
Last updated May 17, 2026 02:41 UTC
-
Gene therapy trial aims to tame severe seizures in kids
Disease control OngoingThis study tests a gene therapy called ETX101 in children aged 6 months to under 7 years with Dravet syndrome, a severe epilepsy. The treatment uses a harmless virus to deliver a working gene to brain cells. The main goals are to check safety and see if it reduces seizures. Only …
Matched conditions: DRAVET SYNDROME
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated May 17, 2026 02:39 UTC
-
New hope for babies with severe epilepsy: drug trial targets seizures in toddlers
Disease control OngoingThis study tests a medicine called fenfluramine in 25 infants aged 1 to 2 years who have Dravet syndrome, a severe form of epilepsy. The goal is to see if the drug is safe and can reduce seizures. Researchers will closely monitor heart health and growth, since the medicine has kn…
Matched conditions: DRAVET SYNDROME
Phase: PHASE3 • Sponsor: UCB BIOSCIENCES, Inc. • Aim: Disease control
Last updated May 17, 2026 02:38 UTC
-
Gene therapy trial aims to tame severe seizures in kids with dravet syndrome
Disease control OngoingThis study tests a gene therapy called ETX101 in 5 children aged 6 months to under 4 years with Dravet syndrome, a severe epilepsy. The treatment uses a harmless virus to deliver a working gene to brain cells, aiming to reduce seizures and improve development. The main goals are …
Matched conditions: DRAVET SYNDROME
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated May 15, 2026 11:55 UTC
-
New hope for dravet syndrome: expanded access to fenfluramine offers seizure control
Disease control APPROVED_FOR_MARKETINGThis study provides fenfluramine to people with Dravet syndrome whose seizures are not controlled by other medications. The goal is to make the drug available and check its safety. Participants must have a genetic diagnosis and have tried all available seizure drugs.
Matched conditions: DRAVET SYNDROME
Sponsor: University of California, Los Angeles • Aim: Disease control
Last updated May 15, 2026 11:54 UTC
-
Hope for dravet syndrome: Long-Term safety trial of STK-001 underway
Disease control OngoingThis study looks at the long-term safety of an experimental drug called zorevunersen (STK-001) in 60 people with Dravet syndrome, a severe form of epilepsy. Participants must have completed a previous STK-001 study. The main goal is to check for side effects, while also tracking …
Matched conditions: DRAVET SYNDROME
Phase: PHASE2 • Sponsor: Stoke Therapeutics, Inc • Aim: Disease control
Last updated May 11, 2026 20:41 UTC
-
Epidiolex liver check: no alarm, just monitoring
Knowledge-focused OngoingThis study watches for possible long-term liver damage in 154 people already taking or starting Epidiolex for certain seizure disorders. Researchers will use blood tests and special scans to check for liver scarring over time. The goal is to understand if the drug can cause chron…
Matched conditions: DRAVET SYNDROME
Phase: PHASE4 • Sponsor: Jazz Pharmaceuticals • Aim: Knowledge-focused
Last updated May 17, 2026 02:43 UTC
-
New study aims to uncover hidden clues to prevent sudden death in dravet syndrome
Knowledge-focused OngoingThis study looks at how repeated seizures may harm breathing and heart control in people with Dravet syndrome, a severe form of epilepsy. Researchers will monitor 92 children and adults over time to find early warning signs that could help prevent sudden unexpected death. The goa…
Matched conditions: DRAVET SYNDROME
Phase: NA • Sponsor: Hospices Civils de Lyon • Aim: Knowledge-focused
Last updated May 14, 2026 12:04 UTC