APLASTIC ANEMIA

This study is checking on patients for up to five years after they finished a previous trial for a drug called romiplostim, which treats aplastic anemia. The goal is to see if the treatment's benefits last long-term and to watch for any delayed side effects or health changes. It …

This study aims to confirm the safety of the drug ATGAM for patients in Japan who have moderate to severe aplastic anemia, a rare condition where the body stops producing enough new blood cells. It will observe a small group of patients for 6 months to monitor for any side effect…

This study is testing a new type of cell therapy for patients with blood cancers or bone marrow diseases who need a stem cell transplant from a partially matched family donor. The goal is to see if adding specially treated immune cells, called 'veto cells,' can help the donor's c…

This study is testing a personalized plan to manage cytomegalovirus (CMV), a common and potentially serious infection, in patients who have received a donor stem cell transplant for blood cancers or disorders. The plan involves closely monitoring the virus level and the patient's…

This study is testing a new, gentler bone marrow transplant procedure for people with dyskeratosis congenita, a rare genetic disorder that causes bone marrow failure. The standard transplant uses harsh drugs and radiation that can worsen lung/liver disease and cancer risk in thes…

This study aims to see if adding methadone to standard morphine pain medication better controls severe mouth pain in children aged 6-18 undergoing stem cell transplants. Researchers will compare pain levels, medication use, and recovery between children receiving the two-drug com…