Personalized dosing for kids with dystonia? new study investigates genetic factors

NCT ID NCT06554288

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study is testing how the drug trihexyphenidyl is processed in the bodies of 40 children aged 5-17 with dystonic cerebral palsy. Researchers want to see if a child's genetic makeup changes how the drug works, which could help create personalized dosing plans. Participants will take the drug for 15 weeks, and the study will measure drug levels, side effects, and how well dystonia symptoms are controlled.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

trihexyphenidyl

What this could lead to

If successful, this could lead to personalized dosing guidelines for trihexyphenidyl in children with dystonia, improving treatment effectiveness and safety.

What could go wrong

This is an early Phase 1 study with only 40 participants, so results may not apply to all children. The focus is on understanding drug metabolism, not on proving the drug works.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

athetoid cerebral palsy cerebral palsy Dystonia dystonic disorder inherited disease susceptibility mixed cerebral palsy

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Mercy Hospital Kansas City

    RECRUITING

    Kansas City, Missouri, 64108, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact