New pill plus chemo shows promise for kids with tough cancers

NCT ID NCT06541262

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tests an experimental pill called silmitasertib combined with standard chemotherapy in children and young adults (under 30) whose solid tumors (like neuroblastoma, Ewing sarcoma, or osteosarcoma) have come back or not responded to treatment. The goal is to find a safe dose and see if the combination can shrink tumors or slow their growth. About 104 participants will be enrolled.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

silmitasertib (CX-4945) taken as a pill, combined with chemotherapy drugs irinotecan, temozolomide, and vincristine

What this could lead to

If it works, this could offer a new treatment option for children and young adults with certain hard-to-treat cancers that have come back.

What could go wrong

This is an early-phase trial (Phase I/II) with only 104 participants, so it's too soon to know if the combination is effective. There may be side effects from adding silmitasertib to standard chemo.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Ewing sarcoma liposarcoma neuroblastoma osteosarcoma rhabdomyosarcoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • All Children's Hospital Johns Hopkins Medicine

    RECRUITING

    St. Petersburg, Florida, 33701, United States

    Contact

    Contact Email: •••••@•••••

  • Arnold Palmer Hospital for Children

    RECRUITING

    Orlando, Florida, 32806, United States

    Contact

    Contact Email: •••••@•••••

  • Cardinal Glennon Children's Medical Center

    RECRUITING

    St Louis, Missouri, 63104, United States

    Contact Email: •••••@•••••

    Contact

  • Children's Medical Center

    RECRUITING

    Dallas, Texas, 75235, United States

    Contact Email: •••••@•••••

    Contact

  • Children's Mercy Hospitals and Clinics

    RECRUITING

    Kansas City, Missouri, 64108, United States

    Contact

    Contact Email: •••••@•••••

  • Hackensack University Medical Center

    RECRUITING

    Hackensack, New Jersey, 07601, United States

    Contact

    Contact Email: •••••@•••••

  • Hasbro Children's Hospital

    RECRUITING

    Providence, Rhode Island, 02903, United States

    Contact

    Contact Email: •••••@•••••

  • Kapiolani Medical Center for Women and Children

    RECRUITING

    Honolulu, Hawaii, 96813, United States

    Contact Email: •••••@•••••

    Contact

  • Monroe Carrell Jr. Children's Hospital at Vanderbilt

    RECRUITING

    Nashville, Tennessee, 37232, United States

    Contact Email: •••••@•••••

    Contact

  • Nicklaus Children's Hospital

    RECRUITING

    Miami, Florida, 33155, United States

    Contact Email: •••••@•••••

    Contact

  • Norton Children's Research Institute/Affiliated with University of Louisville School of Medicine

    RECRUITING

    Louisville, Kentucky, 40202, United States

    Contact Email: •••••@•••••

    Contact

  • Penn State Milton S. Hershey Medical Center and Children's Hospital

    RECRUITING

    Hershey, Pennsylvania, 17033, United States

    Contact Email: •••••@•••••

    Contact

  • Phoenix Children's Hospital

    RECRUITING

    Phoenix, Arizona, 85016, United States

    Contact Email: •••••@•••••

    Contact

  • Primary Children's Hospital

    RECRUITING

    Salt Lake City, Utah, 84113, United States

    Contact Email: •••••@•••••

    Contact

  • Rady Children's Hospital

    RECRUITING

    San Diego, California, 92123, United States

    Contact Email: •••••@•••••

    Contact

  • St. Joseph's Children's Hospital

    RECRUITING

    Tampa, Florida, 33614, United States

    Contact

    Contact Email: •••••@•••••

  • UCSF Benioff Children's Hospital Oakland

    RECRUITING

    Oakland, California, 94609, United States

    Contact Email: •••••@•••••

    Contact

  • UHC Sainte-Justine

    RECRUITING

    Montreal, Quebec, QC H3S 2G4, Canada

    Contact Email: •••••@•••••

    Contact

  • University of Alabama/Children's of Alabama

    RECRUITING

    Birmingham, Alabama, 35233, United States

    Contact Email: •••••@•••••

    Contact

  • University of Florida

    RECRUITING

    Gainesville, Florida, 32611, United States

    Contact Email: •••••@•••••

    Contact

  • Virginia Commonwealth University

    RECRUITING

    Richmond, Virginia, 23284, United States

    Contact

    Contact Email: •••••@•••••