New targeted drug combo aims to curb relapse in kids with rare immune disorder

NCT ID NCT07431060

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 2 times

Summary

This study tests whether adding the targeted drug luvometinib to standard chemotherapy improves outcomes for children with multisystem Langerhans cell histiocytosis (LCH), a rare immune cell disorder. About 120 children aged 0-18 with newly diagnosed, untreated LCH will be randomly assigned to receive either standard chemo alone or chemo plus luvometinib. The goal is to see if the combination reduces disease reactivation and improves survival without major side effects.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Luvometinib (a targeted cancer drug) plus chemotherapy (prednisone, vincristine, mercaptopurine)

What this could lead to

If successful, this combination could offer better disease control and fewer relapses for children with severe multisystem LCH.

What could go wrong

This is an early-stage trial with only 120 participants, so results may not apply to all children. Adding a targeted drug may also increase side effects like skin issues or high triglycerides.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Histiocytosis, Langerhans-Cell Langerhans cell histiocytosis

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Affiliated Hospital of Guizhou Medical University

    RECRUITING

    Guiyang, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Anhui Provincial Children's Hospital

    RECRUITING

    Hefei, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Jiangxi Provincial Children's Hospital

    RECRUITING

    Jiangxi, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Kunming Children's Hospital

    RECRUITING

    Kunming, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The First Affiliated Hospital of Xinjiang Medical University

    RECRUITING

    Ürümqi, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Second Affiliated Hospital of Anhui Medical University

    RECRUITING

    Hefei, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Second Affiliated Hospital of Guangxi Medical University

    RECRUITING

    Nanning, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • West China Second Hospital, Sichuan University

    RECRUITING

    Chengdu, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Xi'an Children's Hospital

    RECRUITING

    Xi'an, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Xi'an Northwest Women's and Children's Hospital

    RECRUITING

    Xi'an, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Zunyi Medical University Affiliated Hospital, Guizhou Provincial Children's Hospital

    RECRUITING

    Zunyi, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••