New hope for rare immune diseases: targeted drug trial launches

NCT ID NCT06153173

First seen Nov 01, 2025 · Last updated Apr 25, 2026 · Updated 30 times

Summary

This study tests a drug called mirdametinib in people aged 2 and older with certain rare immune cell diseases (like Langerhans cell histiocytosis). The goal is to see if it works better and causes fewer side effects than current treatments. About 40 participants will take the drug for up to a year, and doctors will measure how well tumors shrink using scans.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for LANGERHANS CELL HISTIOCYTOSIS (LCH) are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Cincinnati Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.