Halted trial tests potential treatment for genetic form of dementia

NCT ID NCT04374136

Summary

This study tested an investigational drug called AL001 for people who have or are at risk for frontotemporal dementia (FTD) because they carry a specific gene mutation. The goal was to see if the drug could slow or control the progression of the disease. The trial was a large Phase 3 study but was terminated before completion.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • ASST degli Spedali Civili di Brescia - Spedali Civili di Brescia

    Brescia, Italy

  • Box Hill Hospital

    Box Hill, 3128, Australia

  • CHRU Lille

    Lille, France

  • CHU de Bordeaux

    Bordeaux, France

  • Centro Hospitalar E Universitário de Coimbra EPE

    Coimbra, Portugal

  • Centro Hospitalar de Lisboa Norte, EPE - Hospital de Santa Maria

    Lisbon, 1649-035, Portugal

  • Centro Hospitalar do Porto - Hospital de Santo António

    Porto, 4099-001, Portugal

  • Dignity Health

    Phoenix, Arizona, 85013, United States

  • Eginitio University General Hospital of Athens - 1st University Neurology Clinic

    Athens, Attica, 115 28, Greece

  • Emory University

    Atlanta, Georgia, 30329, United States

  • Erasmus MC

    Rotterdam, Netherlands

  • Felix Platter Spital

    Basel, Switzerland

  • Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico

    Milan, Italy

  • Fondazione IRCCS Di Rilievo Nazionale Istituto Nazionale Neurologico Carlo Besta

    Milan, Italy

  • Fundación Para La Lucha Contra Las Enfermedades Neurológicas de La Infancia

    Buenos Aires, 2325, Argentina

  • Groupe Hospitalier Pitié Salpétrière

    Paris, France

  • Hospital CUF Descobertas

    Lisbon, Portugal

  • Hospital Clinic de Barcelona

    Barcelona, Spain

  • Hospital Universitario de Donostia

    Donostia / San Sebastian, Spain

  • Houston Methodist Institute for Academic Medicine

    Houston, Texas, 77030, United States

  • IRCCS - Centro S. Giovanni di Dio Fatebenefratelli

    Brescia, Italy

  • Indiana University Health Neuroscience Center

    Indianapolis, Indiana, 46202, United States

  • Irving Institute for Clinical and Translational Research

    New York, New York, 10032, United States

  • Istanbul University Medical Faculty

    Istanbul, Fatih, 34093, Turkey (Türkiye)

  • Johns Hopkins University School of Medicine

    Baltimore, Maryland, 21205, United States

  • Karolinska Universitetssjukhuset Huddinge - PPDS

    Huddinge, Sweden

  • Mayo Comprehensive Cancer Center - PPDS

    Rochester, Minnesota, 55905, United States

  • Nuovo Ospedale Civile S. Agostino-Estense di Baggiovara

    Baggiovara, Italy

  • Oregon Health and Science University

    Portland, Oregon, 97239, United States

  • PIA Fondazione Panico

    Tricase, Italy

  • Sunnybrook Research Institute - University of Toronto

    Toronto, Canada

  • The Queen Elizabeth Hospital

    Woodville, Australia

  • The University of Western Ontario

    London, Canada

  • UZ Leuven

    Leuven, Vlaams Brabant, 3000, Belgium

  • Uniklinik Köln

    Cologne, 50937, Germany

  • University College London

    London, United Kingdom

  • University General Hospital of Alexandroupolis - Department of Neurology

    Alexandroupoli, Evros, 68100, Greece

  • University Of Cincinnati Gardner Neuroscience institute

    Cincinnati, Ohio, 45219, United States

  • University of California San Diego

    La Jolla, California, 92093-0648, United States

  • University of Colorado

    Aurora, Colorado, 80045, United States

  • University of Kansas Alzheimer's Disease Center

    Fairway, Kansas, 66205, United States

  • University of Pennsylvania

    Philadelphia, Pennsylvania, 19104, United States

  • Universitätsklinikum Ulm

    Ulm, Germany

  • Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States

Conditions

Explore the condition pages connected to this study.