PRADER-WILLI SYNDROME
Clinical trials for PRADER-WILLI SYNDROME explained in plain language.
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Could gut bacteria help kids with rare genetic obesity?
Disease control Recruiting nowThis study looks at whether prebiotics and probiotics (supplements that support healthy gut bacteria) can safely help control appetite and weight gain in 60 children with Prader-Willi syndrome, a rare genetic condition that causes severe obesity. The approach aims to improve gut …
Matched conditions: PRADER-WILLI SYNDROME
Phase: NA • Sponsor: Children's Hospital of Fudan University • Aim: Disease control
Last updated May 26, 2026 05:56 UTC
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New study tests Weight-Loss drug in rare obesity conditions
Disease control Recruiting nowThis study tests the weight-loss drug tirzepatide in young adults aged 18-26 with Prader-Willi syndrome, hypothalamic obesity, or general obesity. Participants take the medication for one year to see how much weight they lose and how other health measures change. The goal is to s…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE4 • Sponsor: Grace Kim • Aim: Disease control
Last updated May 26, 2026 05:55 UTC
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New program aims to get adults with intellectual disability moving
Disease control Recruiting nowThis study tests a program called PACE that helps adults with intellectual disability become more physically active. About 120 adults, their caregivers, and coaches will take part. The program focuses on increasing daily steps and moderate-to-vigorous activity to improve overall …
Matched conditions: PRADER-WILLI SYNDROME
Phase: NA • Sponsor: University of North Carolina, Chapel Hill • Aim: Disease control
Last updated May 20, 2026 11:56 UTC
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New weekly shot targets genetic obesity in early trial
Disease control Recruiting nowThis study tests a new weekly injection called RM-718 in 150 people with obesity, including those with a genetic condition affecting the MC4R pathway (like Prader-Willi syndrome). The main goal is to check safety and how the drug moves through the body. It is an early-phase trial…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE1, PHASE2 • Sponsor: Rhythm Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 19, 2026 11:47 UTC
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New hope for Prader-Willi syndrome: drug targets extreme daytime sleepiness
Symptom relief Recruiting nowThis study tests a medication called pitolisant to see if it can reduce excessive daytime sleepiness in people aged 6 and older with Prader-Willi syndrome. About 134 participants will receive either the drug or a placebo, and researchers will also check if it helps with irritabil…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Harmony Biosciences Management, Inc. • Aim: Symptom relief
Last updated May 26, 2026 05:42 UTC
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New drug aims to curb relentless hunger in rare genetic disorder
Symptom relief Recruiting nowThis early-stage trial tests an experimental drug called CSTI-500 in 12 people with Prader-Willi syndrome, a genetic condition that causes constant, extreme hunger. The study aims to see if the drug is safe and can reduce the urge to overeat. Participants aged 13 to 50 will recei…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE2 • Sponsor: ConSynance Therapeutics • Aim: Symptom relief
Last updated May 18, 2026 12:00 UTC
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Scientists launch largest study on rare imprinting disorders
Knowledge-focused Recruiting nowThis study follows 2000 children and adults with rare genetic conditions called imprinting disorders, such as Silver-Russell and Prader-Willi syndromes. Researchers aim to describe how these conditions affect metabolism over time, including risks for obesity, diabetes, and heart …
Matched conditions: PRADER-WILLI SYNDROME
Sponsor: Institut National de la Santé Et de la Recherche Médicale, France • Aim: Knowledge-focused
Last updated May 26, 2026 05:51 UTC
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New registry aims to shed light on rare diseases
Knowledge-focused Recruiting nowThis study is creating a large database to collect information about people with rare diseases like amyloidosis, sarcoidosis, and many others. Researchers will track patients' health, treatments, and outcomes over time. The goal is to better understand these conditions and improv…
Matched conditions: PRADER-WILLI SYNDROME
Sponsor: Hospital Italiano de Buenos Aires • Aim: Knowledge-focused
Last updated May 26, 2026 05:46 UTC
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Magnetic brain zap targets Out-of-Control hunger in rare disorder
Knowledge-focused Recruiting nowThis study is testing a safe, noninvasive technique called TMS (transcranial magnetic stimulation) to see if it can affect brain areas linked to hunger and fullness in people with Prader-Willi syndrome. Twenty participants will receive TMS and have brain scans before and after. T…
Matched conditions: PRADER-WILLI SYNDROME
Phase: NA • Sponsor: Brigham and Women's Hospital • Aim: Knowledge-focused
Last updated May 15, 2026 11:58 UTC