New drug cocktail takes aim at Hard-to-Treat leukemia

NCT ID NCT06001788

First seen Jun 26, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This early-stage trial is testing a new drug called ziftomenib combined with standard chemotherapy or another targeted drug for people with relapsed or treatment-resistant acute myeloid leukemia (AML) that has specific genetic changes. The main goal is to see if these combinations are safe and tolerable. About 171 participants will receive different treatment combinations to find the best dose and check for side effects.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
ziftomenib (a targeted drug) combined with chemotherapy (FLAG-IDA, low-dose cytarabine) or gilteritinib
What this could lead to
If successful, this could point toward a new combination treatment option for people with hard-to-treat AML who have specific genetic mutations.
What could go wrong
This is an early Phase 1 trial with only 171 participants, focused on safety. It is too soon to know if the combinations will work better than existing treatments, and side effects are unknown.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

Locations

  • Atrium Health Levine Cancer Center

    RECRUITING

    Charlotte, North Carolina, 60201, United States

  • Banner MD Anderson Cancer Center

    RECRUITING

    Gilbert, Arizona, 85234, United States

    Contact Email: •••••@•••••

  • Beth Israel Deaconess Medical Center

    RECRUITING

    Boston, Massachusetts, 02215, United States

  • Colorado Blood Cancer Institute

    RECRUITING

    Denver, Colorado, 80218, United States

  • Emory Healthcare - The Emory Clinic

    RECRUITING

    Atlanta, Georgia, 30322, United States

  • Fondazione Policlinico Universitario Agostino Gemelli IRCCS

    RECRUITING

    Roma, 00168, Italy

  • Froedtert & Medical College Clinics

    RECRUITING

    Milwaukee, Wisconsin, 53226, United States

  • Georgia Cancer Center at Augusta University

    RECRUITING

    Augusta, Georgia, 30912, United States

  • Henry Ford Cancer Institute

    RECRUITING

    Detroit, Michigan, 48202, United States

  • Hospital Universitari Vall d'Hebron

    RECRUITING

    Barcelona, 08035, Spain

  • Hospital Universitari y Politecnic La Fe

    RECRUITING

    Valencia, 46026, Spain

  • Hospital Universitario Central de Asturias

    RECRUITING

    Oviedo, 33011, Spain

  • Hospital Universitario Virgen del Rocío

    RECRUITING

    Seville, 41013, Spain

  • IRCCS Azienda Ospedaliero-Universitaria do Bologna - Policlinico di Sant'Orsola

    RECRUITING

    Bologna, 40138, Italy

  • John Theurer Cancer Center at Hackensack University Medical Center

    RECRUITING

    Hackensack, New Jersey, 07601, United States

  • Karmanos Cancer Institute

    RECRUITING

    Detroit, Michigan, 48201, United States

  • Lehigh Valley Topper Cancer Institute

    WITHDRAWN

    Allentown, Pennsylvania, 18103, United States

  • Loyola University Medical Center

    RECRUITING

    Maywood, Illinois, 60153, United States

  • MD Anderson Cancer Center

    RECRUITING

    Houston, Texas, 77030, United States

  • Memorial Sloan Kettering Cancer Center

    RECRUITING

    New York, New York, 10021, United States

  • Northwell Health, LLC PRIME

    RECRUITING

    Lake Success, New York, 11042, United States

  • OU Health Stephenson Cancer Center

    RECRUITING

    Oklahoma City, Oklahoma, 73104, United States

  • Ospedale Santa Maria delle Croci

    RECRUITING

    Ravenna, 48121, Italy

  • Prisma Health

    RECRUITING

    Greenville, South Carolina, 29615, United States

  • Robert H. Lurie Comprehensive Cancer Center of Northwestern University

    RECRUITING

    Chicago, Illinois, 60611, United States

    Contact Email: •••••@•••••

  • Roswell Park Comprehensive Cancer Center

    RECRUITING

    Buffalo, New York, 14263, United States

  • Simmons Cancer Institute

    WITHDRAWN

    Springfield, Illinois, 62702, United States

  • Smilow Cancer Hospital at Yale New Haven

    RECRUITING

    New Haven, Connecticut, 06511, United States

  • Stony Brook Cancer Center

    RECRUITING

    Stony Brook, New York, 11794, United States

  • Texas Oncology - Baylor Charles A. Sammons Cancer Center

    RECRUITING

    Dallas, Texas, 75246, United States

  • The University of Kansas Cancer Center

    RECRUITING

    Kansas City, Kansas, 66160, United States

  • UC Irvine Health Chao Family Comprehensive Cancer Center

    RECRUITING

    Orange, California, 92868, United States

    Contact Email: •••••@•••••

  • UCLA Health - Bowyer Oncology Center

    RECRUITING

    Los Angeles, California, 90095, United States

  • UH Seidman Cancer Center

    RECRUITING

    Cleveland, Ohio, 44106, United States

  • USC Norris Comprehensive Cancer Center

    RECRUITING

    Los Angeles, California, 90089, United States

  • University of California San Francisco

    RECRUITING

    San Francisco, California, 94115, United States

  • University of Iowa Hospitals & Clinics

    RECRUITING

    Iowa City, Iowa, 52242, United States

  • University of Nebraska Medical Center

    RECRUITING

    Omaha, Nebraska, 68198, United States

  • University of Vermont

    RECRUITING

    Burlington, Vermont, 05401, United States

  • University of Virginia Comprehensive Cancer Center

    RECRUITING

    Charlottesville, Virginia, 22903, United States

  • University of Washington

    RECRUITING

    Seattle, Washington, 98109, United States

  • Vanderbilt University Medical Center

    RECRUITING

    Nashville, Tennessee, 37232, United States

  • Washington University School of Medicine

    RECRUITING

    St Louis, Missouri, 63110, United States

  • Weill Cornell Medical College-NY Presbyterian Hospital

    RECRUITING

    New York, New York, 10065, United States

  • Wilmot Cancer Institute, University of Rochester

    RECRUITING

    Rochester, New York, 14642, United States

    Contact Email: •••••@•••••

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