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New drug VX-670 enters human testing for muscle disease DM1

NCT ID NCT06185764

Recruiting now Disease control Sponsor: Vertex Pharmaceuticals Incorporated Source: ClinicalTrials.gov ↗

First seen Jan 06, 2026 · Last updated Apr 29, 2026 · Updated 18 times

Summary

This early-stage trial tests the safety and tolerability of a new drug, VX-670, in 44 adults with myotonic dystrophy type 1 (DM1). Participants receive either the drug or a placebo in single or multiple doses. The study aims to find the right dose and understand how the drug moves through the body.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Altasciences Montreal

    RECRUITING

    Montreal, Canada

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

  • CHU Research Centre of Quebec

    RECRUITING

    Québec, Canada

  • Centro Clinico NeMO

    RECRUITING

    Milan, Italy

  • Clinical Research Facility, Queen Elizabeth University Hospital

    RECRUITING

    Glasgow, United Kingdom

  • Hopital de Chicoutimi

    RECRUITING

    Chicoutimi, Canada

  • Hospital Universitario y Politécnico La Fe

    RECRUITING

    Valencia, Spain

  • Leonard Wolfson Experimental Neurology Centre CRF

    RECRUITING

    London, United Kingdom

  • Ludwig Maximilians Universitaet Muenchen

    RECRUITING

    München, Germany

  • Maastricht University Medical Center

    RECRUITING

    Maastricht, Netherlands

  • McGIll University

    RECRUITING

    Montreal, Canada

  • Neuromuscular Reference Center Institute of Myology

    RECRUITING

    Paris, France

  • Neuroscience Clinical Trials Unit, Alfred Brain

    RECRUITING

    Melbourne, Australia

  • Royal Hallamshire Hospital

    RECRUITING

    Sheffield, United Kingdom

  • Salford Royal Hospital

    RECRUITING

    Salford, United Kingdom

  • St. George's University Hospital

    RECRUITING

    London, United Kingdom

  • Stanford Neuromuscular Research

    RECRUITING

    San Carlos, California, 94070, United States

  • Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg

    RECRUITING

    Leuven, Belgium

  • University of Florida Clinical Research Center

    RECRUITING

    Gainesville, Florida, 32608, United States

  • University of Kansas Medical Center

    RECRUITING

    Fairway, Kansas, 66205, United States

  • University of Ottawa

    RECRUITING

    Ottawa, Canada

  • University of Pennsylvania

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Virginia Commonwealth University (Sanger Hall)

    RECRUITING

    Richmond, Virginia, 23298, United States

  • Wake Forest Baptist Health

    RECRUITING

    Winston-Salem, North Carolina, 27104, United States

  • Washington University School of Medicine / St. Louis Children's Hospital

    RECRUITING

    St Louis, Missouri, 63110, United States

  • Wesley Research Institute

    RECRUITING

    Auchenflower, Australia

Conditions

Explore the condition pages connected to this study.

MYOTONIC DYSTROPHY TYPE 1 (DM1)