Milder transplant method aims to help young patients with rare blood diseases
NCT ID NCT01962415
First seen Jan 04, 2026 · Last updated Jun 14, 2026 · Updated 29 times
Summary
This study is testing a less intense chemotherapy and radiation regimen before a stem cell transplant for children and young adults up to age 55 with non-cancerous blood disorders like immune deficiencies, anemias, and metabolic diseases. The goal is to see if this gentler preparation can reduce deaths and side effects while still allowing donor cells to take hold. About 100 participants will receive a transplant from umbilical cord blood, bone marrow, or blood stem cells and be followed for at least a year.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Phone: •••-•••-•••• Email: •••••@•••••
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Locations
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UPMC Children's Hospital of Pittsburgh
RECRUITINGPittsburgh, Pennsylvania, 15224, United States
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