HEREDITARY ANEMIAS
Clinical trials for HEREDITARY ANEMIAS explained in plain language.
Never miss a new study
Get alerted when new HEREDITARY ANEMIAS trials appear
Sign up with your email to follow new studies for HEREDITARY ANEMIAS, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Gentler transplant offers hope for rare disease patients
Disease control Recruiting nowThis study is collecting information on a less intense stem cell transplant method for people with inherited disorders like immune deficiencies, sickle cell disease, or metabolic diseases. It aims to see how well patients recover, how often the transplant is successful, and how l…
Matched conditions: HEREDITARY ANEMIAS
Sponsor: Paul Szabolcs • Aim: Disease control
Last updated Mar 31, 2026 12:11 UTC
-
Gentler transplant offers hope for kids with rare, Life-Limiting diseases
Disease control Recruiting nowThis study is testing a less intense, potentially safer stem cell transplant procedure for children and young adults with serious inherited disorders like sickle cell disease, immune deficiencies, and metabolic diseases. The goal is to see if using lower doses of chemotherapy bef…
Matched conditions: HEREDITARY ANEMIAS
Phase: PHASE2 • Sponsor: Paul Szabolcs • Aim: Disease control
Last updated Mar 16, 2026 15:26 UTC