Milder chemo before stem cell transplant shows promise for rare blood disorders

adrenoleukodystrophy alpha-mannosidosis autoimmune lymphoproliferative syndrome beta thalassemia Chediak-Higashi syndrome chronic granulomatous disease congenital amegakaryocytic thrombocytopenia 1 Congenital Bone Marrow Failure Syndromes Crohn disease Diamond-Blackfan anemia Gaucher disease hereditary anemia hyper-IgM syndrome immune dysregulation-polyendocrinopathy-enteropathy-X-linked syndrome inborn error of immunity inborn errors of metabolism inflammatory bowel disease Krabbe disease leukocyte adhesion deficiency 1 Lymphohistiocytosis, Hemophagocytic metachromatic leukodystrophy Mucopolysaccharidosis I osteopetrosis Primary Immunodeficiency Diseases rheumatoid arthritis severe combined immunodeficiency sickle cell disease Sudden Infant Death syndromic disease Wiskott-Aldrich syndrome