HEREDITARY ANEMIAS
Clinical trials for HEREDITARY ANEMIAS explained in plain language.
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Gentler transplant approach aims to save lives from rare diseases
Disease control Recruiting nowThis study is testing a milder chemotherapy treatment given before a stem cell transplant for children and young adults with serious inherited disorders of the blood, immune system, or metabolism. The goal is to see if using lower-dose chemotherapy reduces severe side effects and…
Matched conditions: HEREDITARY ANEMIAS
Phase: PHASE2 • Sponsor: Paul Szabolcs • Aim: Disease control
Last updated Apr 01, 2026 23:26 UTC
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Gentler transplant offers hope for rare disease patients
Disease control Recruiting nowThis study is collecting information on a less intense stem cell transplant method for people with inherited disorders like immune deficiencies, sickle cell disease, or metabolic diseases. It aims to see how well patients recover, how often the transplant is successful, and how l…
Matched conditions: HEREDITARY ANEMIAS
Sponsor: Paul Szabolcs • Aim: Disease control
Last updated Mar 31, 2026 12:11 UTC