Cure My Disease

Don't miss your cure!

 Log in / Sign up

No treatment, just tracking: PROPEL study watches how kids with achondroplasia grow

NCT ID NCT04035811

Completed Knowledge-focused Sponsor: QED Therapeutics, a BridgeBio company Source: ClinicalTrials.gov ↗

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study followed 271 children with achondroplasia, ages 2.5 to 17, to understand their growth, medical issues, and quality of life over time. No medication or treatment was given. The goal was to gather natural history data to help design future clinical trials.

This is an AI summary of the original study and may miss details. Read our disclaimer.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for ACHONDROPLASIA are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Conditions

The condition(s) this trial relates to.

achondroplasia bone disorder Dwarfism hereditary disease Mucopolysaccharidosis IV musculoskeletal system disorder osteochondrodysplasia

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

ACHONDROPLASIA

Contacts and locations

Locations

  • Benioff Children's Hospital Oakland

    Oakland, California, 94609, United States

  • Birmingham Children's Hospital

    Birmingham, United Kingdom

  • Bristol Royal Hospital for Children

    Bristol, England, United Kingdom

  • Children's Hospital - London Health Sciences Center

    London, Ontario, N6A 5W9, Canada

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Cincinnati Children's Hospital

    Cincinnati, Ohio, 45229, United States

  • Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlino

    Milan, 20122, Italy

  • Haukeland Universitetssjukehus

    Bergen, 5009, Norway

  • Hopital Femme Mere Enfant

    Lyon, France

  • Hopital Necker-Enfants Malades

    Paris, France

  • Hopital des Enfants

    Toulouse, France

  • Hospital Universitario La Paz

    Madrid, 24086, Spain

  • Hospital Universitario Virgen de la Victoria

    Málaga, Spain

  • Hospital de Pediatría SAMIC Prof. Dr. Juan P. Garrahan

    Buenos Aires, Argentina

  • Johns Hopkins School of Medicine

    Baltimore, Maryland, 21211, United States

  • KK Women's and Children's Hospital

    Singapore, 229899, Singapore

  • Manchester University Children's Hospital

    Manchester, United Kingdom

  • Murdoch Children's Research Institute

    Parkville, Australia

  • Nemours Alfred I. Dupont Hospital for Children

    Wilmington, Delaware, 19803, United States

  • Oslo Universitetssykehus

    Oslo, 0372, Norway

  • Otto-von-Guericke-University Magdeburg Medical Fakulty

    Magdeburg, 39120, Germany

  • Queen Elizabeth University Hospital

    Glasgow, United Kingdom

  • Rare Disease Unit Fondazione Policlinico A Gemelli IRCCS

    Rome, 00168, Italy

  • Sheffield Children's Hospital

    Sheffield, United Kingdom

  • St. Thomas' Hospital

    London, United Kingdom

  • Stollery Children's Hospital

    Edmonton, Alberta, T6G 2H7, Canada

  • University of Missouri

    Columbia, Missouri, 65211, United States

  • University of Montreal

    Montreal, Quebec, H3C 3J7, Canada

  • University of Ottawa

    Ottawa, Ontario, K1N 6N5, Canada

  • University of Wisconsin Madison - Waisman Center Bone Dysplasia Clinic

    Madison, Wisconsin, 53705, United States

  • Vanderbilt University Medical Center

    Nashville, Tennessee, 37232, United States

  • Vithas Hospital San Jose

    Barcelona, 08305, Spain

More trials for these conditions

Other studies related to the condition(s) this trial covers.