Premature baby brain drug fails in large trial

NCT ID NCT01378273

First seen Jun 26, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This Phase 3 trial tested whether giving erythropoietin (Epo) soon after birth could reduce death or severe disability in extremely premature infants (born at 24-27 weeks). Over 900 babies were enrolled and followed until age 2. Unfortunately, Epo did not significantly lower the risk of death or severe neurodevelopmental impairment compared to placebo.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

erythropoietin (Epo)

What this could lead to

If it worked, this could reduce the risk of death or severe developmental problems in extremely premature babies.

What could go wrong

This large Phase 3 trial found no significant benefit on the primary outcome. The treatment also carries risks like blood clots and high red blood cell counts.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Premature Birth

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • All Childrens Hospital

    St. Petersburg, Florida, 33701, United States

  • Beth Israel Deaconess Hospital

    Boston, Massachusetts, 02215, United States

  • Children's Hospital of Minnesota, MN

    Minneapolis, Minnesota, 55404, United States

  • Children's Hospital of Minnesota, St. Paul

    Saint Paul, Minnesota, 55102, United States

  • Children's Hospital of the University of Illinois

    Chicago, Illinois, 60612, United States

  • Florida Hospital

    Orlando, Florida, 32804, United States

  • Johns Hopkins

    Baltimore, Maryland, 21224, United States

  • Maia Fareri Children's Hospital

    Valhalla, New York, 10595, United States

  • Methodist Children's Hospital

    San Antonio, Texas, 78229, United States

  • Prentice Women's Hospital

    Chicago, Illinois, 60611, United States

  • South Miami Hospital

    Miami, Florida, 33146, United States

  • University of Arkansas

    Little Rock, Arkansas, 72202, United States

  • University of Florida

    Gainesville, Florida, 32610, United States

  • University of Louisville

    Louisville, Kentucky, 40202, United States

  • University of Minnesota Amplatz Children's Hospital

    Minneapolis, Minnesota, 55455, United States

  • University of New Mexico Children's Hospital

    Albuquerque, New Mexico, 87131, United States

  • University of Utah

    Salt Lake City, Utah, 84108, United States

  • University of Washington

    Seattle, Washington, 98195, United States

  • Wake Forest School of Medicine

    Winston-Salem, North Carolina, 27157, United States