Can a common antioxidant help babies with a rare liver disease? first safety trial begins

NCT ID NCT06260566

First seen Jun 24, 2026 · Last updated Jun 27, 2026 · Updated 2 times

Summary

This early-phase study tests whether infants with biliary atresia can tolerate oral N-Acetylcysteine (NAC) mixed into applesauce. Twelve infants will first receive plain applesauce, then NAC at increasing doses. The goal is to see if they can keep the medicine down without vomiting. If successful, this could lead to larger studies on NAC as a treatment to improve bile flow after Kasai surgery.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

N-Acetylcysteine (NAC) given orally mixed with applesauce

What this could lead to

If NAC is well-tolerated, it could pave the way for larger studies testing whether it helps improve bile flow after Kasai surgery in infants with biliary atresia.

What could go wrong

This is a very early phase 1 trial with only 12 infants, focused on tolerability, not effectiveness. NAC may cause vomiting or other side effects, and even if tolerated, it may not improve the disease.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

biliary atresia cholestasis

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

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