Scientists track rare liver diseases in kids to unlock clues

NCT ID NCT01148550

First seen Oct 31, 2025 · Last updated May 08, 2026 · Updated 24 times

Summary

This study follows children and young adults with rare mitochondrial liver diseases to learn how these conditions progress over time. Researchers collect medical data and samples like blood and tissue to build a biobank for future studies. The goal is to better understand the diseases, improve diagnosis, and predict outcomes. No new treatments are tested; this is an observational study.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Ann & Robert H. Lurie Children's Hospital

    Chicago, Illinois, 60611, United States

  • Children's Healthcare of Atlanta - Emory University

    Atlanta, Georgia, 30322, United States

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Children's Hospital Los Angeles

    Los Angeles, California, 90027, United States

  • Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

  • Johns Hopkins School of Medicine

    Baltimore, Maryland, 21287, United States

  • Mount Sinai Medical Center

    New York, New York, 10029, United States

  • Riley Hospital for Children

    Indianapolis, Indiana, 46202, United States

  • Seattle Children's Hospital

    Seattle, Washington, 98105, United States

  • Texas Children's Hospital (Baylor College of Medicine)

    Houston, Texas, 77030, United States

  • The Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • UPMC Children's Hospital of Pittsburgh

    Pittsburgh, Pennsylvania, 15224, United States

  • University of California at San Francisco (UCSF)

    San Francisco, California, 94143, United States

  • University of Utah

    Salt Lake City, Utah, 84113, United States

  • Washington University School of Medicine

    St Louis, Missouri, 63110, United States

Conditions

Explore the condition pages connected to this study.