New hope for myositis patients: long-term drug safety trial underway

NCT ID NCT05979441

ENROLLING_BY_INVITATION Disease control Sponsor: argenx Source: ClinicalTrials.gov ↗

First seen Nov 01, 2025 · Last updated May 15, 2026 · Updated 25 times

Summary

This study looks at the long-term safety of a drug called efgartigimod for adults with a group of muscle diseases known as idiopathic inflammatory myopathy (IIM). Only people who completed an earlier study of this drug can join. Participants will receive the drug for up to 51 months, followed by a 56-day safety check. The goal is to see if the drug remains safe and tolerable over time.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for DERMATOMYOSITIS are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • ATTIKON University General Hospital - Neurology

    Athens, 12462, Greece

  • AZ Sint-Lucas - Campus Sint-Lucas - Neurology

    Ghent, 9000, Belgium

  • Aintree University Hospital - Liverpool University Hospitals NHS Foundation Trust

    Liverpool, L9 7AL, United Kingdom

  • Amsterdam UMC Research BV

    Amsterdam, 1105 AZ, Netherlands

  • Attune Health Research, Inc

    Beverly Hills, California, 90039, United States

  • Austin Neuromuscular Center (National Neuromuscular Research Institute, PLLC)

    Austin, Texas, 78759, United States

  • Aversi Clinic

    Tbilisi, 0160, Georgia

  • Azienda Ospedaliero Universitaria Consorziale Policlinico

    Bari, 70124, Italy

  • Azienda Ospedaliero Universitaria Pisana - Ospedale Santa Chiara - Rheumatology

    Pisa, 56126, Italy

  • Azienda sanitaria universitaria Friuli Centrale - ASUFC

    Udine, 33100, Italy

  • Centro Dermatologico Schejtman

    San Miguel, B1663GKT, Argentina

  • Centro Hospitalar do Porto - Hospital Santo Antonio

    Porto, 4099-001, Portugal

  • Centro Medico Privado de Reumatologia

    San Miguel de Tucumán, 4000, Argentina

  • Centrum Wsparcia Badan Klinicznych Pomorskiego Uniwersytetu Medycznego w Szczecinie (CWBK PUM) - Rheumatology

    Szczecin, 71-252, Poland

  • Charite Universitaetsmedizin Berlin - Campus Charite Mitte (CCM) - Rheumatology

    Berlin, 10117, Germany

  • China Medical University (CMU) - First Affiliated Hospital

    Shenyang, 110001, China

  • Chung Shan Medical University Hospital

    Taichung, 402, Taiwan

  • Clinica San Juan de Dios - sede Arequipa - Rheumatology

    Arequipa, 4000, Peru

  • Clinical Center of Serbia

    Belgrade, 11000, Serbia

  • Copenhagen University Hospital-Rigshospitalet University Hospital

    Copenhagen, 2100, Denmark

  • Cyprus Institute of Neurology and Genetics

    Nicosia, 2371, Cyprus

  • Emory Healthcare - Emory Clinic - Rheumatology

    Atlanta, Georgia, 30322, United States

  • Faculty Of Medicine, Khon Kaen University

    Khon Kaen, 40002, Thailand

  • First Affiliated Hospital (Henan Medical University - First Affiliated Hospital)-Zhengzhou University

    Zhengzhou, 450052, China

  • Fondazione Policlinico Universitario Agostino Gemelli - Neurology

    Roma, 168, Italy

  • Framingham Centro Medico

    La Plata, B1902COS, Argentina

  • Hospital Angeles Clinica Londres

    Mexico City, 06700, Mexico

  • Hospital Universitari i Politecnic La Fe de Valencia - Neurology

    Valencia, 46026, Spain

  • Hospital Universitario 12 de Octubre

    Madrid, 28041, Spain

  • Hospital de la Santa Creu i Sant Pau

    Barcelona, 08041, Spain

  • Huashan Hospital Affiliated to Fudan University

    Shanghai, 200040, China

  • Institute of Rheumatology

    Belgrade, 11000, Serbia

  • Institute of Science Tokyo Hospital

    Tokyo, 113-8519, Japan

  • Instituto Peruano Del Hueso Y La Articulacion Sac-Privado-Lima,Centro De Investigacion Iphar

    Lima, 27, Peru

  • Investigaciones Clinicas S.A.C.

    Lima, 33, Peru

  • Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) - Ospedale San Raffaele Hospital

    Milan, 20132, Italy

  • Japan Community Healthcare Organization Chukyo Hospital

    Nagoya, 457-8510, Japan

  • Juntendo University Hospital

    Bunkyō City, 113-8431, Japan

  • Karolinska Universitestssjukhus Solna

    Solna, 17176, Sweden

  • King Chulalongkorn Memorial Hospital - Neurology

    Bangkok, 10330, Thailand

  • Klinikum der Universitaet Ulm

    Ulm, 89081, Germany

  • LLC MediClub Georgia

    Tbilisi, 0160, Georgia

  • Mayo Clinic - Florida - Neurology

    Jacksonville, Florida, 32224, United States

  • Medical Centre Artmed

    Plovdiv, 4002, Bulgaria

  • Multiprofile hospital for active treatment Kaspela EOOD

    Plovdiv, 4002, Bulgaria

  • National and Kapodistrian University of Athens - Eginition Hospital

    Athens, 115 28, Greece

  • National and Kapodistrian University of Athens - School of Health Sciences - Faculty of Medicine

    Athens, 115 27, Greece

  • Nerve And Muscle Center Of Texas

    Houston, Texas, 77030, United States

  • Neuromuscular Clinical and Research Center - Neurology

    Phoenix, Arizona, 85028, United States

  • New Hospitals

    Tbilisi, 0162, Georgia

  • Northern Care Allicance NHS Foundation Trust - Salford Royal - Rheumatology

    Salford, M6 8HD, United Kingdom

  • Northwell Health Physician Partners Rheumatology

    Great Neck, New York, 11021, United States

  • Northwestern Medicine - Northwestern Memorial Hospital

    Chicago, Illinois, 60611, United States

  • Oregon Health and Science University

    Portland, Oregon, 97239, United States

  • Ospedale Sant'Andrea Hospital

    Roma, 00189, Italy

  • Peking Union Medical College Hospital

    Beijing, 100730, China

  • Peking University Third Hospital

    Beijing, 100191, China

  • Phramongkutklao Hospital

    Bangkok, 10400, Thailand

  • Ramathibodi hospital

    Bangkok, 10400, Thailand

  • Reference Center Neuro-Muscular Diseases - CHU Paris Group Hospitalier La Pitie Salpetriere-Charles Foix

    Paris, 75013, France

  • Revmatologicky Ustav

    Prague, 12850, Czechia

  • Rheumazentrum Ruhrgebiet

    Herne, 44649, Germany

  • Santaros University Clinic

    Vilnius, 08410, Lithuania

  • Seoul National University Hospital

    Seoul, 03080, South Korea

  • Shanghai Jiao Tong University School of Medicine - Renji Hospital - Shanghai Institute of Digestive Disease (SIDD)

    Shanghai, 200001, China

  • Sichuan Provincial Academy of Medical Sciences and Sichuan Provincial People's Hospital

    Chengdu, 610072, China

  • Siriraj Hospital, Mahidol University of Internal medicine

    Bangkok, 10700, Thailand

  • The First Medical Center

    Tbilisi, 0180, Georgia

  • The Ohio State University

    Columbus, Ohio, 43201, United States

  • The Royal Free Hospital

    London, NW3 2QG, United Kingdom

  • The University of Tokyo Hospital

    Bunkyō City, 113-8655, Japan

  • Tirol Kliniken - A.o. Landeskrankenhaus Innsbruck - Neurology

    Innsbruck, 6020, Austria

  • UCI Health - ALS and Neuromuscular Center - Neurology

    Orange, California, 92868, United States

  • UCSF Health - ALS and Neurodegenerative Disease Center - Dermatology

    San Francisco, California, 94143, United States

  • UF Health - Rheumatology Medical Specialties Medical Plaza

    Gainesville, Florida, 32610, United States

  • USK-WAM Centralny Szpital Weteranow - Szpital Kniniczny ul. Zeromskiego 113 - Rheumatology

    Lodz, 90-549, Poland

  • Universitaetsklinikum Hamburg-Eppendorf

    Hamburg, 20246, Germany

  • Universitaetsklinikum Tuebingen (UKT)

    Tübingen, 72076, Germany

  • Universitair Ziekenhuis Leuven Gasthuisberg Campus

    Leuven, 3000, Belgium

  • Universitatsmedizin Mannheim GmbH

    Mannheim, 68167, Germany

  • University College Dublin (UCD) - St. Vincent's University Hospital (SVUH)

    Dublin, D04 T6F4, Ireland

  • University of North Carolina (UNC) School of Medicine

    Chapel Hill, North Carolina, 27514, United States

  • University of Pittsburgh Medical Center

    Pittsburgh, Pennsylvania, 15261, United States

  • University of South Florida (USF) - Morsani Center (USF Health Carol and Frank Morsani Center for Advanced Healthcare)

    Tampa, Florida, 33616, United States

  • Wakayama Medical University Hospital

    Wakayama, 641-8510, Japan

  • Yale Cancer Center-Yale University School Of Medicine

    New Haven, Connecticut, 06520, United States

Conditions

Explore the condition pages connected to this study.