Early safety trial of ION269 for Alzheimer's in down syndrome ends after just one participant

NCT ID NCT06673069

First seen Jun 26, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This early-stage study tested a drug called ION269 in adults with Down syndrome who also showed signs of Alzheimer's disease. The goal was to check if the drug was safe and tolerable when injected into the spinal fluid. Only one person took part, and the study was stopped early, so we have very little information about how well it works or what the risks might be.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

ION269 (given as an injection into the spinal fluid)

What this could lead to

If successful, this could point toward a treatment to slow Alzheimer's disease in people with Down syndrome.

What could go wrong

This was a very early, tiny Phase 1 safety study with only 1 participant, and it was terminated early. It is far too small to know if the drug works or is safe.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Alzheimer disease Down syndrome

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Ionis Investigative Site

    Indianapolis, Indiana, 46202, United States

  • Ionis Investigative Site

    Kansas City, Kansas, 66205, United States

  • Ionis Investigative Site

    Lexington, Kentucky, 40536, United States

  • Ionis Investigative Site

    St Louis, Missouri, 63110, United States

  • Ionis Investigative Site

    Madison, Wisconsin, 53705, United States

  • Ionis Investigative Site

    Barcelona, 08041, Spain