One-Time gene therapy could shield lungs in rare disease
NCT ID NCT06996756
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This early-stage study tests a gene therapy for people with alpha-1 antitrypsin deficiency, a condition that can damage the lungs. The treatment is given once through a vein and aims to produce a special protein that protects the lungs. Researchers will check safety and measure protein levels in the blood. The study involves 16 adults with mild to moderate lung disease.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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WCMC Department of Genetic Medicine
RECRUITINGNew York, New York, 10021, United States
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