Trikafta's hidden effects: new study probes metabolism and microbiome in CF patients

NCT ID NCT07363304

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study follows 150 cystic fibrosis patients starting the drug combination Trikafta (ETI) to see how it affects their metabolism, DNA methylation, and gut bacteria. Researchers will measure blood fats, sugars, and immune markers, and link them to drug levels. The goal is to understand why some patients develop side effects like high cholesterol or liver problems, and to find ways to personalize dosing.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Elexacaftor-Tezacaftor-Ivacaftor (Trikafta/Kaftrio)

What this could lead to

If successful, this could help doctors personalize ETI dosing to reduce side effects like high cholesterol or liver issues, improving long-term care for cystic fibrosis patients.

What could go wrong

This is an observational study, not a treatment trial. It won't prove if ETI works or is safe, only track changes in the body. Results may not apply to all patients.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

cystic fibrosis

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Azienda Ospedaliera Universitaria Meyer Istituto di Ricovero e Cura a Carattere Scientifico

    RECRUITING

    Florence, 5016, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Centro per la Fibrosi Cistica, Azienda Universitaria Ospedaliera Consorziale Policlinico

    NOT_YET_RECRUITING

    Bari, Bari, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Centro per la Fibrosi Cistica, Ospedale Infantile Regina Margherita

    NOT_YET_RECRUITING

    Torino, Torino, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Dipartimento di Pediatria, Centro Fibrosi Cistica, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

    NOT_YET_RECRUITING

    Milan, Milano, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Ospedale pediatrico Bambino Gesù, IRCCS, Dipartimento Pediatrico Universitario Ospedaliero, UOC Pneumologia e Fibrosi Cistica

    NOT_YET_RECRUITING

    Roma, Roma, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Unità Pediatrica, Dipartimento di Scienze Mediche Traslazionali, Centro di Riferimento Regionale per la Fibrosi Cistica, Università degli Studi di Napoli Federico II

    NOT_YET_RECRUITING

    Naples, Napoli, Italy

    Contact Phone: •••-•••-•••• Email: •••••@•••••