Could modern CF drugs make daily inhaled treatments obsolete?

NCT ID NCT07696338

First seen Jul 10, 2026 · Last updated Jul 10, 2026

Summary

This trial investigates whether children and teens with cystic fibrosis who are already taking highly effective modulator therapy can safely use inhaled airway clearance treatments only when they have a respiratory illness, instead of every day. Participants stop their usual daily hypertonic saline or dornase alfa for a short run-in period, then are randomly assigned to either daily use or as-needed use for one year. The study measures lung function to see if both approaches keep lungs equally healthy.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
hypertonic saline and dornase alfa
What this could lead to
If successful, this could show that daily inhaled treatments are no longer needed for many children with cystic fibrosis who take modern modulators, reducing treatment burden.
What could go wrong
This is a mid-sized trial in children with mild lung disease; results may not apply to those with more severe disease. The study may also find that as-needed use leads to worse lung function over time.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • All Children's Hospital

    St. Petersburg, Florida, 33701, United States

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    Chicago, Illinois, 60611, United States

    Contact Email: •••••@•••••

  • Baylor College of Medicine

    Houston, Texas, 77030, United States

  • Boston Children's Hospital

    Boston, Massachusetts, 02115, United States

  • CF Centre BC Children's Hospital (Vancouver, Canada)

    Vancouver, British Columbia, V6H3V4, Canada

    Contact Email: •••••@•••••

  • CF Centre Hospital for Sick Children (Toronto, ON)

    Toronto, Ontario, M5G1X8, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • CHOC Children's Hospital

    Orange, California, 92868, United States

  • Children's Healthcare of Atlanta and Emory University

    Atlanta, Georgia, 30322, United States

  • Children's Hospital Colorado

    Aurora, Colorado, 80045, United States

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Children's Hospital of Pittsburgh of UPMC

    Pittsburgh, Pennsylvania, 15224, United States

    Contact Email: •••••@•••••

  • Children's Hospitals and Clinics of Minnesota

    Minneapolis, Minnesota, 55404, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's Mercy Kansas City

    Kansas City, Missouri, 64108, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's Wisconsin

    Milwaukee, Wisconsin, 53226, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Childrens Hospital Los Angeles

    Los Angeles, California, 90027, United States

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • Dayton Children's Hospital

    Dayton, Ohio, 45404, United States

  • John Hopkins Hospital

    Baltimore, Maryland, 21287, United States

  • Medical University of South Carolina

    Charleston, South Carolina, 29425, United States

    Contact Email: •••••@•••••

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Oregon Health & Sciences University

    Portland, Oregon, 97239, United States

  • Providence Medical Group, Cystic Fibrosis Clinic - Pediatrics

    Spokane, Washington, 99204, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Queen Elizabeth II Hospital Halifax Adult CF Centre

    Halifax, Nova Scotia, Canada

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center

    Cleveland, Ohio, 44106, United States

  • Riley Hospital for Children

    Indianapolis, Indiana, 46202, United States

  • Seattle Children's Hospital

    Seattle, Washington, 98105, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • St. Louis Children's Hospital

    St Louis, Missouri, 63110, United States

  • Stanford University Medical Center

    Palo Alto, California, 94025, United States

  • The Children's Hospital Alabama, University of Alabama at Birmingham

    Birmingham, Alabama, 35233, United States

  • The Minnesota Cystic Fibrosis Center

    Minneapolis, Minnesota, 55455, United States

  • Tucson Cystic Fibrosis Center

    Tucson, Arizona, 85724, United States

  • University of Iowa

    Iowa City, Iowa, 52242, United States

  • University of Michigan, Michigan Medicine

    Ann Arbor, Michigan, 48109, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of North Carolina at Chapel Hill

    Chapel Hill, North Carolina, 27599, United States

    Contact Email: •••••@•••••

  • University of Rochester Medical Center Strong Memorial

    Rochester, New York, 14642, United States

  • University of Texas Southwestern / Children's Health

    Dallas, Texas, 75207, United States

  • University of Virginia

    Charlottesville, Virginia, 22904, United States

  • University of Wisconsin

    Madison, Wisconsin, 53792, United States

  • Virginia Commonwealth University

    Richmond, Virginia, 23219, United States

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