New drug trial targets rare kidney disease at genetic root

NCT ID NCT05448755

First seen Mar 31, 2026 · Last updated May 13, 2026 · Updated 5 times

Summary

This early study tested a drug called ELX-02 in 3 people with Alport syndrome, a genetic kidney disease. The goal was to see if the drug is safe and if it can reduce protein in the urine, a sign of kidney damage. Participants received daily injections for 8 weeks and were followed for 3 months after.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Great Ormond Street Hospital

    London, WC1N 3JH, United Kingdom

  • Monash Medical Center

    Clayton, Victoria, 3168, Australia

  • Royal Children's Hospital

    Parkville, Victoria, 3051, Australia

  • Royal Free Hospital

    London, NW3 2QG, United Kingdom

Conditions

Explore the condition pages connected to this study.