Massive study aims to unlock genetic secrets of rare liver disease in kids

NCT ID NCT00345553

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study is collecting medical information, genetic material, and body fluid samples from over 1,200 children with biliary atresia, a rare liver disease. The goal is to find genes that cause the disease and understand how it progresses in children who still have their own liver. No new treatments are being tested; instead, researchers hope to learn more about the disease to guide future care.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

What this could lead to
If successful, this could help identify genes linked to biliary atresia and better predict how the disease progresses in children who haven't had a liver transplant.
What could go wrong
This is an observational study, not a treatment trial, so it won't directly improve health. It may take years to yield useful insights, and genetic findings may not apply to all patients.

This is an AI summary of the original study and may miss details. Read our disclaimer.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    RECRUITING

    Chicago, Illinois, 60614, United States

  • Children's Healthcare of Atlanta - Emory University

    RECRUITING

    Atlanta, Georgia, 30322, United States

  • Children's Hospital Colorado

    RECRUITING

    Aurora, Colorado, 80045, United States

  • Children's Hospital Medical Center

    RECRUITING

    Cincinnati, Ohio, 45229, United States

  • Children's Hospital of Los Angeles

    RECRUITING

    Los Angeles, California, 90027, United States

  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Hospital for Sick Children

    COMPLETED

    Toronto, Ontario, M5G 1X8, Canada

  • Johns Hopkins School of Medicine

    COMPLETED

    Baltimore, Maryland, 21287, United States

  • Mount Sinai Medical Center

    COMPLETED

    New York, New York, 10029, United States

  • Riley Children's Hospital

    COMPLETED

    Indianapolis, Indiana, 46202, United States

  • Seattle Children's Hospital

    RECRUITING

    Seattle, Washington, 98105, United States

  • Texas Children's Hospital (Baylor College of Medicine)

    RECRUITING

    Houston, Texas, 77030, United States

  • UPMC Children's Hospital of Pittsburgh

    COMPLETED

    Pittsburgh, Pennsylvania, 15224, United States

  • University of California at San Francisco

    COMPLETED

    San Francisco, California, 94143, United States

  • University of Utah

    RECRUITING

    Salt Lake City, Utah, 84113, United States

  • Washington University School of Medicine

    COMPLETED

    St Louis, Missouri, 63110, United States

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