PRADER-WILLI SYNDROME
Clinical trials for PRADER-WILLI SYNDROME explained in plain language.
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Promising drug targets severe hunger in rare genetic disorder
Disease control OngoingThis study tests a drug called setmelanotide in people aged 6 to 65 with Prader-Willi syndrome, a condition that causes severe obesity and constant hunger. About 18 participants will receive a daily injection for up to 52 weeks to see if it safely reduces body weight and controls…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE2 • Sponsor: Rhythm Pharmaceuticals, Inc. • Aim: Disease control
Last updated Jun 16, 2026 12:50 UTC
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New hope for rare hunger disorder: drug shows promise in Long-Term trial
Disease control TerminatedThis study tests whether ARD-101 can safely reduce extreme hunger and food-related behaviors in people with Prader-Willi syndrome over 12 months. About 90 participants who completed a prior study will take the drug daily and visit the clinic regularly. The goal is to improve qual…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Aardvark Therapeutics, Inc. • Aim: Disease control
Last updated Jun 15, 2026 19:06 UTC
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New drug under observation for rare genetic disorder
Disease control ENROLLING_BY_INVITATIONThis study follows about 200 people with Prader-Willi syndrome who are taking or starting VYKAT XR. Researchers will track side effects and how the drug affects their health over time. The goal is to gather more safety information, not to test if the drug cures the condition.
Matched conditions: PRADER-WILLI SYNDROME
Sponsor: Soleno Therapeutics, Inc. • Aim: Disease control
Last updated Jun 10, 2026 13:27 UTC
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New safety study for Prader-Willi drug pitolisant enrolls 150 patients
Disease control ENROLLING_BY_INVITATIONThis study looks at how safe the drug pitolisant is for people with Prader-Willi syndrome. It includes 150 people who have already taken pitolisant in an earlier study. Researchers will track any side effects that happen during treatment and for 30 days after the last dose.
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Harmony Biosciences Management, Inc. • Aim: Disease control
Last updated May 27, 2026 23:06 UTC
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Hope for rare hunger disorder: new drug enters final testing
Symptom relief TerminatedThis study tests whether ARD-101 can reduce the intense, constant hunger (hyperphagia) seen in people with Prader-Willi syndrome. About 90 participants will take either the drug or a placebo daily for 12 weeks. Caregivers will track changes in hunger-related behaviors using a que…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Aardvark Therapeutics, Inc. • Aim: Symptom relief
Last updated Jun 15, 2026 19:03 UTC
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Could a gentle zap calm severe outbursts? new trial for Prader-Willi syndrome
Symptom relief OngoingThis study tests a small device that gently stimulates a nerve in the ear (vagus nerve) to see if it can safely reduce temper outbursts in people with Prader-Willi syndrome. About 102 participants aged 10 to 40 will use the device daily. The goal is to improve emotional control a…
Matched conditions: PRADER-WILLI SYNDROME
Phase: PHASE3 • Sponsor: Foundation for Prader-Willi Research • Aim: Symptom relief
Last updated Jun 11, 2026 12:09 UTC