HEREDITARY ANGIOEDEMA
Clinical trials for HEREDITARY ANGIOEDEMA explained in plain language.
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New pill shows promise for controlling rare swelling disorder
Disease control OngoingThis study looks at the long-term safety of an oral medication called KVD900 for treating sudden swelling attacks in people with hereditary angioedema (HAE) types I or II. About 145 adolescents and adults who previously took part in a related study will take KVD900 as needed for …
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE3 • Sponsor: KalVista Pharmaceuticals, Ltd. • Aim: Disease control
Last updated May 17, 2026 08:12 UTC
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New drug shows promise in preventing painful swelling attacks for HAE patients
Disease control OngoingThis study tests a medicine called donidalorsen for people with hereditary angioedema (HAE), a condition that causes sudden, painful swelling. The goal is to see if the drug is safe and effective over the long term at preventing these attacks and improving quality of life. About …
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE3 • Sponsor: Ionis Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 17, 2026 08:01 UTC
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Gene therapy aims to stop painful swelling attacks in rare disease
Disease control OngoingThis study tests a new treatment called NTLA-2002 for people with hereditary angioedema (HAE), a condition that causes sudden, painful swelling attacks. The goal is to see if the drug can reduce the number of attacks compared to a placebo. About 80 participants aged 16 and older …
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE3 • Sponsor: Intellia Therapeutics • Aim: Disease control
Last updated May 17, 2026 08:00 UTC
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New hope for kids with rare swelling disorder: daily pill may prevent attacks
Disease control OngoingThis study tests a daily medication called berotralstat to prevent sudden swelling attacks in children aged 2 to 12 with hereditary angioedema (HAE). About 29 children will take the pill to see how it works in their bodies and if it is safe. The goal is to find the right dose to …
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE3 • Sponsor: BioCryst Pharmaceuticals • Aim: Disease control
Last updated May 17, 2026 08:00 UTC
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New hope for swelling disorder: experimental drug enters human trials
Disease control OngoingThis study tests an experimental drug called ADX-324 for hereditary angioedema, a genetic condition that causes sudden, severe swelling attacks. The first part involves healthy volunteers to check safety, and the second part includes people with the disease to see how the drug wo…
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE1, PHASE2 • Sponsor: ADARx Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 15, 2026 11:57 UTC
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New HAE drug switch study aims for safer monthly prevention
Disease control OngoingThis study looks at whether it is safe for people aged 12 and older with hereditary angioedema (HAE) to switch from their current preventive medicine to a new monthly injection called garadacimab. About 18 participants will receive garadacimab for around 3 months, and researchers…
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE4 • Sponsor: CSL Behring • Aim: Disease control
Last updated May 15, 2026 11:56 UTC
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Gene therapy aims to stop painful swelling attacks in rare disease
Disease control OngoingThis study tests a new treatment called NTLA-2002 for adults with hereditary angioedema (HAE), a condition that causes sudden, painful swelling attacks. The therapy uses gene-editing to reduce a protein that triggers attacks. Researchers are checking safety and how well it works …
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE1, PHASE2 • Sponsor: Intellia Therapeutics • Aim: Disease control
Last updated May 14, 2026 12:02 UTC
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Gene therapy for HAE: how does it hold up over time?
Disease control ENROLLING_BY_INVITATIONThis study follows about 100 people who previously received the experimental gene therapy NTLA-2002 for hereditary angioedema (HAE). Researchers will monitor participants for long-term safety and check how well the treatment continues to prevent HAE attacks. The goal is to unders…
Matched conditions: HEREDITARY ANGIOEDEMA
Sponsor: Intellia Therapeutics • Aim: Disease control
Last updated May 12, 2026 13:39 UTC
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New pill could quickly stop swelling attacks in hereditary angioedema
Disease control ENROLLING_BY_INVITATIONThis study is testing an oral medication called deucrictibant for quickly treating swelling attacks in people with hereditary angioedema (HAE), including dangerous throat swelling. It involves 150 adults who have previously been in related studies or are new to the drug. The goal…
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE2, PHASE3 • Sponsor: Pharvaris Netherlands B.V. • Aim: Disease control
Last updated May 11, 2026 20:53 UTC
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Study offers ongoing HAE treatment access for prior trial participants
Disease control ENROLLING_BY_INVITATIONThis study gives people with hereditary angioedema (HAE) who were in earlier berotralstat trials continued access to the medication. About 139 participants will receive the drug and be monitored for side effects and safety. The goal is to keep providing treatment while gathering …
Matched conditions: HEREDITARY ANGIOEDEMA
Phase: PHASE3 • Sponsor: BioCryst Pharmaceuticals • Aim: Disease control
Last updated May 05, 2026 11:53 UTC