DUCHENNE MUSCULAR DYSTROPHY (DMD)
Clinical trials for DUCHENNE MUSCULAR DYSTROPHY (DMD) explained in plain language.
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New hope for boys with devastating muscle disease
Disease control Recruiting nowThis study is testing a new drug called ENTR-601-44 for Duchenne muscular dystrophy (DMD), a severe genetic muscle-wasting disease. It aims to see if the drug is safe, find the right dose, and check if it helps produce a needed muscle protein. The trial is for boys and young men …
Matched conditions: DUCHENNE MUSCULAR DYSTROPHY (DMD)
Phase: PHASE1, PHASE2 • Sponsor: Entrada Therapeutics, Inc. • Aim: Disease control
Last updated Mar 31, 2026 12:11 UTC
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New hope for DMD: experimental drug aims to restore muscle protein
Disease control Recruiting nowThis study is testing a new medicine called ENTR-601-45 for boys and young men with Duchenne muscular dystrophy (DMD), a rare muscle-wasting disease. The first part checks the medicine's safety and finds the best dose, while the second part looks at how well it works. Researchers…
Matched conditions: DUCHENNE MUSCULAR DYSTROPHY (DMD)
Phase: PHASE1, PHASE2 • Sponsor: Entrada Therapeutics, Inc. • Aim: Disease control
Last updated Mar 30, 2026 14:29 UTC
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First human test: can mRNA fix broken muscles in DMD kids?
Disease control Recruiting nowThis early study is testing whether a new treatment called SPOT-mRNA03 is safe for boys with Duchenne muscular dystrophy (DMD). The treatment delivers genetic instructions to help muscles produce a missing protein called dystrophin. Six boys aged 2-6 will receive the treatment th…
Matched conditions: DUCHENNE MUSCULAR DYSTROPHY (DMD)
Phase: EARLY_PHASE1 • Sponsor: Shanghai Siponuoyin Biotechnology Co Ltd • Aim: Disease control
Last updated Mar 27, 2026 12:39 UTC
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Smart insoles could reveal hidden clues in Kids' steps
Knowledge-focused Recruiting nowThis study aims to develop better ways to measure how diseases like Duchenne Muscular Dystrophy (DMD) and Spinal Muscular Atrophy (SMA) progress over time. Researchers will have 106 children wear special 'smart' insoles in their shoes to track their walking patterns both in a lab…
Matched conditions: DUCHENNE MUSCULAR DYSTROPHY (DMD)
Sponsor: Columbia University • Aim: Knowledge-focused
Last updated Mar 30, 2026 14:33 UTC
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Could a simple pee test speed up the search for DMD treatments?
Knowledge-focused Recruiting nowThis study aims to find a better way to measure muscle damage in boys with Duchenne or Becker Muscular Dystrophy (DMD/BMD). Researchers are testing if a protein called titin, found in urine, changes after physical activity and relates to disease severity. The goal is to create a …
Matched conditions: DUCHENNE MUSCULAR DYSTROPHY (DMD)
Phase: NA • Sponsor: Children's Hospital of Philadelphia • Aim: Knowledge-focused
Last updated Mar 30, 2026 14:28 UTC
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Smart baby clothes and ankle sensors aim to predict muscle disease progression
Knowledge-focused Recruiting nowThis study aims to understand how motor skills develop in very young children diagnosed with spinal muscular atrophy (SMA) or Duchenne muscular dystrophy (DMD). It will follow 100 children under age 4 for up to 30 months using special wearable sensors at home, like a smart jumpsu…
Matched conditions: DUCHENNE MUSCULAR DYSTROPHY (DMD)
Phase: NA • Sponsor: Centre Hospitalier Universitaire de Liege • Aim: Knowledge-focused
Last updated Mar 25, 2026 14:09 UTC
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Scientists test gut hormones to protect bones in children with rare muscle diseases
Knowledge-focused Recruiting nowThis study aims to understand if two natural gut hormones, GIP and GLP-2, can help slow down bone loss in children with spinal muscular atrophy, cerebral palsy, or Duchenne muscular dystrophy. Researchers will measure bone health markers in the blood of 8 children who use wheelch…
Matched conditions: DUCHENNE MUSCULAR DYSTROPHY (DMD)
Phase: NA • Sponsor: University of Copenhagen • Aim: Knowledge-focused
Last updated Mar 12, 2026 13:51 UTC
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First human test for new DMD drug begins
Knowledge-focused Recruiting nowThis is a very early study to check if a new drug called GRT6019 is safe for people. It will be given to 24 healthy male volunteers for four weeks to see how their bodies react and process it. The main goal is to find the right dose and understand side effects before testing in p…
Matched conditions: DUCHENNE MUSCULAR DYSTROPHY (DMD)
Phase: PHASE1 • Sponsor: Grünenthal GmbH • Aim: Knowledge-focused
Last updated Feb 27, 2026 15:18 UTC