DUCHENNE MUSCULAR DYSTROPHY (DMD)

This early-stage study tests the safety of a new drug, RAG-18, in 12 boys aged 4-15 with Duchenne muscular dystrophy. The drug is given through a vein, and researchers will check for side effects, how the body processes the drug, and whether it helps slow muscle damage. The goal …

This study looks at the long-term safety and effects of the drug SAT-3247 in people with Duchenne muscular dystrophy (DMD) who have taken it before. Up to 10 participants will take the drug for about 12 months total. Researchers will check for side effects and measure changes in …

This study tests an 8-week dual-tasking program for 16 boys aged 6–12 with Duchenne muscular dystrophy (DMD). The program combines physical and mental exercises, like walking while counting backward, to improve thinking, balance, and daily living skills. Participants are randomly…

This pilot study tests a small device worn on the ear that gently stimulates a nerve to reduce inflammation in children with Duchenne muscular dystrophy (DMD). The study involves 20 boys aged 5-17 who will use the device at home for one week. Researchers will measure changes in b…

This study looks at how the muscles in the upper arm change in people with Duchenne muscular dystrophy (DMD). Researchers will use a device called MyotonPRO to measure muscle tone, stiffness, and elasticity in the biceps, triceps, and other arm muscles. About 56 participants with…

This study is testing a virtual reality game designed specifically for people with Duchenne muscular dystrophy. Six participants will play the game once using a VR headset and hand tracking. Researchers will measure how easy and enjoyable the game is, and whether it causes any di…

This early-stage trial tests the safety and how the body handles a new drug called GRT6019 in 24 healthy men. The drug is being developed for Duchenne muscular dystrophy, but this study only checks for side effects and drug levels in the blood. Participants take the drug for 4 we…