New hope for DMD: Long-Term drug trial aims to preserve muscle function
NCT ID NCT07573631
First seen May 09, 2026 · Last updated May 24, 2026 · Updated 3 times
Summary
This study looks at the long-term safety and effects of a weekly IV drug called BMN 351 in people with Duchenne muscular dystrophy (DMD) whose genetic makeup allows for exon 51 skipping. Participants must have completed a prior study of the same drug. The goal is to see if the drug is safe over time and if it helps maintain physical abilities like walking and climbing stairs.
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This is a summary of
the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Fondazione Serena ETS - Centro Clinico NeMO Milano
Milan, Italy
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Great Ormond Street Hospital NHS Foundation Trust
London, WC1N 3JH, United Kingdom
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Hospital Sant Joan de Deu
Barcelona, 08950, Spain
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Hospital Viamed Santa Angela De la Cruz
Seville, 41013, Spain
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Leids Universitair Medisch Centrum
Leiden, 2333 ZA, Netherlands
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UOC Fase I - Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore
Rome, Italy
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Yeditepe University Kosuyolu Hospital
Istanbul, Turkey, Turkey (Türkiye)
Conditions
Explore the condition pages connected to this study.