Repurposed drug offers new hope for genetic form of ALS

This study is testing whether a drug called acamprosate is safe and might help slow the progression of ALS (amyotrophic lateral sclerosis) in people who have a specific genetic mutation in the C9orf72 gene. Thirty participants will take the drug as a pill for 24 weeks while researchers monitor their health, symptoms, and disease progression. The main goal is to check for safety, but researchers will also look for early signs that the drug might help control the disease.