Encoded Therapeutics
Clinical trials sponsored by Encoded Therapeutics, explained in plain language.
-
Gene therapy breakthrough for rare childhood epilepsy?
Disease control OngoingThis study tests a new gene therapy called ETX101 in 5 children with Dravet syndrome, a severe form of epilepsy. The treatment aims to reduce seizures and improve development by delivering a working gene to brain cells. The study is early-stage (Phase 1/2) and focuses on safety, …
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated May 26, 2026 12:10 UTC
-
Gene therapy trial aims to tame severe seizures in kids
Disease control OngoingThis study tests a gene therapy called ETX101 in 4 children with Dravet syndrome, a severe epilepsy disorder. The treatment uses a harmless virus to deliver a working copy of the SCN1A gene. The goal is to see if it safely reduces seizures and improves communication skills.
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated May 26, 2026 12:02 UTC