Gene therapy trial aims to tame severe seizures in kids
NCT ID NCT06112275
First seen Nov 16, 2025 · Last updated May 23, 2026 · Updated 25 times
Summary
This study tests a gene therapy called ETX101 in 4 children with Dravet syndrome, a severe epilepsy disorder. The treatment uses a harmless virus to deliver a working copy of the SCN1A gene. The goal is to see if it safely reduces seizures and improves communication skills.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Genom att skicka in godkänner du våra Användarvillkor
Locations
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The Royal Children's Hospital
Melbourne, Australia
Conditions
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