Breakthrough gene therapy trial offers hope for children with severe epilepsy
Disease control
Recruiting now
This study is testing a gene therapy called ETX101 for children with Dravet syndrome, a severe form of epilepsy. Researchers are checking if the treatment is safe and if it can reduce seizure frequency and improve development. The trial includes infants as young as 6 months up to…
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated Mar 31, 2026 12:11 UTC