Encoded Therapeutics
Clinical trials sponsored by Encoded Therapeutics, explained in plain language.
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Gene therapy trial offers hope for kids with severe epilepsy
Disease control OngoingThis early-stage study is testing a one-time gene therapy called ETX101 in young children with Dravet syndrome, a severe form of genetic epilepsy. The main goals are to see if the treatment is safe and if it can reduce the number and severity of seizures over one year. The study …
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated Mar 17, 2026 13:09 UTC
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Gene therapy trial offers hope for children with devastating seizure disorder
Disease control OngoingThis early-stage study is testing a one-time gene therapy called ETX101 in young children (6 months to 4 years old) with a severe form of genetic epilepsy called Dravet Syndrome. The goal is to see if delivering a corrected gene directly to the brain is safe and can help reduce s…
Phase: PHASE1, PHASE2 • Sponsor: Encoded Therapeutics • Aim: Disease control
Last updated Mar 04, 2026 15:29 UTC